Gene Editing of the Ube3a Antisense-Transcript in an Angelman Syndrome Mouse Model

被引：0
|
作者：
Schmid, Ralf S. [1 ]
Deng, Xuefeng [1 ]
Msackyi, Msema [1 ]
Wilson, James M. [1 ]
机构：
[1] Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA
来源：
MOLECULAR THERAPY | 2020年 / 28卷 / 04期
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D O I：
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中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
934
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页码：405 / 405
页数：1
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