Preliminary results of a phase II clinical trial of Genz-112638 in patients with type I Gaucher disease

被引：1

作者：

Peterschmitt, Judith ^{[1
,8
]}

Lukina, Elena ^{[2
,8
]}

Watman, Nora ^{[3
,8
]}

Banikazemi, Maryam ^{[4
,8
]}

Iastrebner, Marcelo ^{[5
,8
]}

Rosenbaum, Hanna ^{[6
,8
]}

Zimran, Ari ^{[7
,8
]}

Arreguin, Elsa Avila ^{[7
,8
]}

O'Brien, Fanny ^{[1
,8
]}

Smith, Sharon ^{[1
,8
]}

Puga, Ana Cristina ^{[1
,8
]}

机构：

[1] Genzyme Corp, Cambridge, MA USA

[2] Russian Acad Med Sci, Hematol Res Ctr, Moscow, Russia

[3] Hosp Ramos Mejia, Buenos Aires, DF, Argentina

[4] NYU, New York, NY USA

[5] Inst Argentino Diagnost & Tratamiento, Buenos Aires, DF, Argentina

[6] Rambam Med Ctr, Haifa, Israel

[7] Shaare Zedek Med Ctr, Jerusalem, Israel

[8] Seguro Social Hosp Especialidades, Inst Mexicano, Col La Raza, Mexico

来源：

MOLECULAR GENETICS AND METABOLISM | 2008年 / 93卷 / 02期

关键词：

D O I：

10.1016/j.ymgme.2007.10.085

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：S32 / S33

页数：2

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