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Raras CIBERER, Madrid, Spain Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USASevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Hosp Infantil Univ Nino Jesus HIUNJ, Hematol & Hemoterapia, Fdn Invest Biomed, Madrid, Spain Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USALlanos, Lucia论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Inst Invest Sanitaria Fdn Jimenez Diaz, Madrid, Spain Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USAPerez de Camino Gaisse, Begona论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Inst Invest Sanitaria Fdn Jimenez Diaz, Madrid, Spain Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USASanchez, Sol论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Inst Invest Sanitaria Fdn Jimenez Diaz, Madrid, Spain Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USAGlader, Bert论文数: 0 引用数: 0 h-index: 0机构: Lucile Packard Childrens Hosp, Palo Alto, CA USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USAChien, May论文数: 0 引用数: 0 h-index: 0机构: Lucile Packard Childrens Hosp, Palo Alto, CA USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USAQuintana Bustamante, Oscar论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Unidad Mixta Terapias Avanzadas, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USABeard, Brian C.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USALaw, Kenneth M.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USAZeini, Miriam论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USAChoi, Grace论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USANicoletti, Eileen论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USARao, Gayatri R.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USAGrazia Roncarolo, Maria论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Ctr Definit & Curat Med, Stanford, CA 94305 USA Lucile Packard Childrens Hosp, Palo Alto, CA USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USABueren, Juan A.论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Unidad Mixta Terapias Avanzadas, Madrid, Spain Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USASchwartz, Jonathan D.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Unidad Innovac Biomed, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Rocket Pharmaceut Inc, Cranbury, NJ USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USASegovia, Jose C.论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Unidad Mixta Terapias Avanzadas, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Unidad Innovac Biomed, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USA
- [38] Lentiviral mediated gene therapy for pyruvate kinase deficiency: Interim results of a global phase 1 study for adult and pediatric patientsHUMAN GENE THERAPY, 2021, 32 (19-20) : A25 - A25Lorenzo, J. L. Lopez论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainShah, A. J.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Ctr Definit & Curat Med, Stanford, CA USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplan & Re, Stanford, CA USA Stanford Childrens Hosp, Palo Alto, CA USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainNavarro, S.论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol, Inst Innovaci Biomed, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainSevilla, J.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed HIUNJ, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainLlanos, L.论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainGaisse, B. P. de Camino论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainSanchez, S.论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainGlader, B.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplan & Re, Stanford, CA USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainChien, M.论文数: 0 引用数: 0 h-index: 0机构: Stanford Childrens Hosp, Palo Alto, CA USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainBustamante, O. Quintana论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol, Inst Innovaci Biomed, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainBeard, B. C.论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed HIUNJ, Madrid, Spain Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainZeini, M.论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed HIUNJ, Madrid, Spain Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainChoi, G.论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed HIUNJ, Madrid, Spain Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainNicoletti, E.论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed HIUNJ, Madrid, Spain Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainRao, G. R.论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed HIUNJ, Madrid, Spain Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainRoncarolo, M. G.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplan & Re, Stanford, CA USA Stanford Childrens Hosp, Palo Alto, CA USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainBueren, J. A.论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol, Inst Innovaci Biomed, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainSchwartz, J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed HIUNJ, Madrid, Spain Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainSegovia, J. C.论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol, Inst Innovaci Biomed, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, Spain
- [39] Lentiviral Mediated Gene Therapy for Pyruvate Kinase Deficiency: Updated Results of a Global Phase 1 Study for Adult and Pediatric PatientsMOLECULAR THERAPY, 2021, 29 (04) : 42 - 43Lopez Lorenzo, Jose Luis论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainShah, Ami J.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Ctr Definit & Curat Med, Stanford, CA 94305 USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USA Stanford Childrens Hosp, Palo Alto, CA USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainNavarro, Susana论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainSevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainLlanos, Lucia论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainPerez Camino de Gaisse, Begona论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainSanchez, Sol论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainGlader, Bertil论文数: 0 引用数: 0 h-index: 0机构: Stanford Childrens Hosp, Palo Alto, CA USA Stanford Univ, Dept Pediat, Div Hematol Oncol, Sch Med, Stanford, CA 94305 USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainChien, May论文数: 0 引用数: 0 h-index: 0机构: Stanford Childrens Hosp, Palo Alto, CA USA Stanford Univ, Dept Pediat, Div Hematol Oncol, Sch Med, Stanford, CA 94305 USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainQuintana-Bustamante, Oscar论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Inst Innovac Biomed, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainBeard, Brian C.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainLaw, Kenneth M.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainZeini, Miriam论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainChoi, Grace论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainNicoletti, Eileen论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainRao, Gayatri R.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainRoncarolo, Maria Grazia论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Ctr Definit & Curat Med, Stanford, CA 94305 USA Stanford Univ, Sch Med, Div Pediat Hematol Oncol Stem Cell Transplant & R, Stanford, CA 94305 USA Stanford Childrens Hosp, Palo Alto, CA USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainBueren, Juan A.论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Inst Innovac Biomed, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainSchwartz, Jonathan D.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainSegovia, Jose C.论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz, Unidad Mixta Terapias Avanzadas, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Inst Innovac Biomed, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, Spain
- [40] LENTIVIRAL-MEDIATED GENE THERAPY FOR SEVERE PYRUVATE KINASE DEFICIENCY: RESULTS FROM AN ONGOING GLOBAL PHASE 1 STUDYBONE MARROW TRANSPLANTATION, 2023, 58 (SUPP1) : 275 - 276Lopez Lorenzo, Jose Luis论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainShah, Ami论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Stanford, CA USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainSevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus HIUNJ, Fdn invest Biomed, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainNavarro, Susana论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainLlanos, Lucia论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, Spainde Camino Gaisse, Begona Perez论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainSanchez, Sol论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Fdn Jimenez Diaz, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainZubicaray, Josune论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus HIUNJ, Fdn invest Biomed, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainGlader, Bertil论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Stanford, CA USA Lucile Packard Childrens Hosp, Palo Alto, CA USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainChien, May论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Stanford, CA USA Lucile Packard Childrens Hosp, Palo Alto, CA USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainQuintana Bustamante, Oscar论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainZeini, Miriam论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainChoi, Grace论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainNicoletti, Eileen论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainRao, Gayatri论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainRoncarolo, Maria Grazia论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Stanford, CA USA Lucile Packard Childrens Hosp, Palo Alto, CA USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainBueren, Juan论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, SpainSchwartz, Jonathan论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Hosp Univ Fdn Jimenez Diaz, Madrid, SpainCarlos Segovia, Jose论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid, Spain Hosp Univ Fdn Jimenez Diaz, Madrid, Spain