Enzyme replacement therapy and monitoring for children with type 1 Gaucher disease: Consensus recommendations

被引：77
|
作者：
Charrow, J
Andersson, HC
Kaplan, P
Kolodny, EH
Mistry, P
Pastores, G
Prakash-Cheng, A
Rosenbloom, BE
Scott, CR
Wappner, RS
Weinreb, NJ
机构：
[1] Childrens Mem Hosp, Div Genet, Chicago, IL 60614 USA
[2] Northwestern Univ, Feinberg Sch Med, Dept Pediat, Chicago, IL 60611 USA
[3] Tulane Univ, Sch Med, Dept Pediat, New Orleans, LA 70118 USA
[4] Childrens Hosp Philadelphia, Dept Pediat, Philadelphia, PA 19104 USA
[5] Univ Penn, Philadelphia, PA 19104 USA
[6] NYU, Sch Med, Dept Neurol, New York, NY USA
[7] Yale Univ, Sch Med, Dept Med, New Haven, CT 06510 USA
[8] Mt Sinai Sch Med, Dept Human Genet, New York, NY USA
[9] Cedars Sinai Med Ctr, Dept Hematol & Oncol, Los Angeles, CA 90048 USA
[10] Univ Washington, Sch Med, Dept Pediat, Seattle, WA 98195 USA
[11] James Whitcomb Riley Hosp Children, Dept Pediat, Indianapolis, IN 46202 USA
[12] James Whitcomb Riley Hosp Children, Dept Med & Mol Genet, Indianapolis, IN 46202 USA
[13] Indiana Univ, Indianapolis, IN 46204 USA
[14] Univ Hosp, Dept Hematol, Tamarac, FL USA
来源：
JOURNAL OF PEDIATRICS | 2004年 / 144卷 / 01期
关键词：
D O I：
10.1016/j.jpeds.2003.10.067
中图分类号：
R72 [儿科学];
学科分类号：
100202 ;
摘要：
[No abstract available]
引用
收藏
页码：112 / 120
页数：9
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