Towards Clinical Translation of Hematopoietic Cell Gene Editing for Treating Hyper-IgM Type 1

被引：0
|
作者：
Vavassori, Valentina [1 ,2 ]
Mercuri, Elisabetta [1 ]
Marcovecchio, Genni [1 ]
Castiello, Maria Carmina [1 ,3 ]
Canarutto, Daniele [1 ,2 ,4 ]
Asperti, Claudia [1 ]
Jacob, Aurelien [1 ]
Albano, Luisa [1 ]
Fontana, Elena [5 ]
Scanziani, Eugenio [5 ]
Radrizzani, Marina [1 ,3 ]
Villa, Anna [1 ]
Genovese, Pietro [6 ]
Naldini, Luigi [1 ,2 ]
机构：
[1] IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy, Milan, Italy
[2] Univ Vita Salute San Raffaele, Milan, Italy
[3] CNR, Milan, Italy
[4] IRCCS San Raffaele Sci Inst, Pediat Immunohematol & Bone Marrow Transplantat U, Milan, Italy
[5] Humanitas, Milan, Italy
[6] Boston Childrens Hosp, Boston, MA USA
来源：
BLOOD | 2021年 / 138卷
关键词：
D O I：
10.1182/blood-2021-148572
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
3978
引用
收藏
页数：3
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