Nusinersen in Infants who Initiate Treatment in a Presymptomatic Stage of Spinal Muscular Atrophy: Interim Results from the Phase 2 NURTURE Study

被引：0
|
作者：
Butterfield, R.
De Vivo, D.
Bertini, E.
Hwu, W-L
Crawford, T.
Swoboda, K.
Finkel, R.
Kirschner, J.
Kuntz, N.
Parsons, J.
Ryan, M.
Topaloglu, H.
Ben Omran, T.
Sansone, V
Jong, Y-J
Shu, F.
Johnson, K.
Foster, R.
Bhan, I
Fradette, S.
Farwell, W.
机构：
来源：
ANNALS OF NEUROLOGY | 2019年 / 86卷
关键词：
Neuromuscular Disorders; Rare Diseases;
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
165
引用
收藏
页码：S117 / S117
页数：1
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