Long-term efficacy and safety of viltolarsen in the treatment of Duchenne muscular dystrophy

被引：0
|
作者：
Clemens, P. [1 ]
Connolly, A. [2 ]
Harper, A. [3 ]
Mah, J. [4 ]
McDonald, C. [5 ]
Rao, V. [6 ]
Smith, E. [7 ]
Zaidman, C. [8 ]
Nakagawa, T. [9 ]
Hoffman, E. [10 ]
机构：
[1] Univ Pittsburgh, Pittsburgh, PA USA
[2] Nationwide Childrens Hosp, Columbus, OH USA
[3] Childrens Hosp Richmond, Richmond, VA USA
[4] Univ Calgary, Calgary, AB, Canada
[5] Univ Calif Davis, Sacramento, CA 95817 USA
[6] Lurie Childrens Hosp Chicago, Chicago, IL USA
[7] Duke Univ, Med Ctr, Durham, NC USA
[8] Washington Univ, St Louis, MO 63110 USA
[9] NS Pharma, Paramus, NJ USA
[10] SUNY Binghamton, Sch Pharm, Binghamton, NY USA
来源：
NEUROMUSCULAR DISORDERS | 2021年 / 31卷
关键词：
D O I：
10.1016/j.nmd.2021.07.165
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
EP.140
引用
收藏
页码：S91 / S91
页数：1
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