IMPROVEMENTS IN MAJOR CLINICAL EVENTS IN CHILDREN TREATED WITH TRIHEPTANOIN FOR LONG-CHAIN FATTY ACID OXIDATION DISORDERS (LC-FAOD)

被引：0
|
作者：
Ray, Kathryn [1 ]
Pisani, Laura [1 ]
Lu, Xiaoxiao [1 ]
Vockley, Jerry [2 ]
机构：
[1] Ultragenyx Pharmaceut Inc, Novato, CA USA
[2] Univ Pittsburgh, Sch Med, UPMC Childrens Hosp Pittsburgh, Pittsburgh, PA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2022年 / 135卷 / 04期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
75
引用
收藏
页码：295 / 296
页数：2
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