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- [41] Nusinersen, an antisense oligonucleotide drug for spinal muscular atrophy [J]. Nature Neuroscience, 2017, 20 : 497 - 499
- [46] Safety, Tolerability, and Effect of Nusinersen in Non-ambulatory Adults With Spinal Muscular Atrophy [J]. FRONTIERS IN NEUROLOGY, 2021, 12
- [48] Study on the efficacy, safety, and biomarkers of nusinersen in type II and III spinal muscular atrophy in children [J]. FRONTIERS IN PEDIATRICS, 2023, 11