Measurement properties of the Fabry Disease Patient Reported Outcome (FD-PRO), a new instrument to measure symptoms in Fabry disease

被引：1
|
作者：
Hamed, Alaa [1 ]
DasMahapatra, Pronabesh [1 ]
Iaconangelo, Charlie [2 ]
Serrano, Daniel [2 ]
Gwaltney, Chad [3 ]
机构：
[1] Sanofi Genzyme, Cambridge, MA USA
[2] Pharmerit, Bethesda, MD USA
[3] Gwaltney Consulting, Westerly, RI USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2019年 / 126卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2018.12.159
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
143
引用
收藏
页码：S67 / S67
页数：1
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