Establishing the content validity of the Fabry Disease-Patient Reported Outcome (FD-PRO) for adolescent patients with Fabry disease

被引：0
|
作者：
Lyn, Nicole [1 ]
Warsi, Ibrahim [1 ]
Whyte, Julie [2 ]
Witherspoon, Brooke [2 ]
Blatt, Elliott [2 ]
DasMahapatra, Pronabesh [1 ]
机构：
[1] Sanofi Genzyme, Cambridge, MA USA
[2] Endpoint Outcomes, Boston, MA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2022年 / 135卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2021.11.200
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
185
引用
收藏
页码：S78 / S78
页数：1
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