Lentiviral vectors for in vivo gene therapy of metachromatic leukodystrophy

被引:0
|
作者
Consiglio, A
Dolcetta, D
Follenzi, A
Luca, T
Marchesini, S
Gritti, A
Vescovi, A
Naldini, L
Bordignon, C
机构
[1] San Raffaele Telethon Inst Gene Therapy, HSR TIGET, Milan, Italy
[2] Univ Turin, Inst Canc Res & Treatment, Turin, Italy
[3] Univ Brescia, Dept Biomed Sci & Biotechnol, Brescia, Italy
[4] Hosp San Raffaele, Stem Cell Res Inst, I-20132 Milan, Italy
关键词
gene therapy; metabolic disease; metachromatic leukodystrophy;
D O I
暂无
中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
摘要
引用
收藏
页码:5 / 5
页数:1
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