Compassionate use of lentiviral gene therapy for metachromatic leukodystrophy

被引：0

作者：

Orchard, Paul J. ^{[1
]}

Gupta, Ashish ^{[1
]}

Adang, Laura A. ^{[2
]}

Braun, Jennifer ^{[1
]}

Pillai, Nishitha R. ^{[1
]}

Lund, Troy ^{[1
]}

Eisengart, Julie B. ^{[1
]}

机构：

[1] Univ Minnesota, Minneapolis, MN USA

[2] Childrens Hosp Philadelphia, Philadelphia, PA USA

来源：

MOLECULAR GENETICS AND METABOLISM | 2024年 / 141卷 / 02期

关键词：

D O I：

10.1016/j.ymgme.2023.107989

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

250

引用

页数：1

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