Results of a family survey on healthcare resource needs in children with neuronal ceroid lipofuscinosis type 2 (CLN2) disease in the US and Canada

被引：0
|
作者：
Rastogi, Sarang [1 ]
Conner, Therese [2 ]
Cook, Francesca [1 ]
Fernandez, Vivian [1 ]
Kirby, Tracy [3 ]
机构：
[1] REGENXBIO Inc, Rockville, MD USA
[2] Xcenda, Palm Harbor, FL USA
[3] BDSRA, Columbus, OH USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2020年 / 129卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2019.11.354
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
345
引用
收藏
页码：S135 / S135
页数：1
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