Hematopoietic stem cell based gene therapy for the treatment of metachromatic leukodystrophy: Towards clinical testing

被引：0
|
作者：
Biffi, Alessandro
Capotondo, Alessia [1 ]
Cesani, Martina [1 ]
Montini, Eugenio [1 ]
Plati, Tiziana [1 ]
Benedicenti, Fabrizio [1 ]
Tononi, Laura [3 ]
Marchesini, Sergio [3 ]
Sessa, Maria [1 ]
Bordignon, Claudio [1 ,2 ]
Roncarolo, Maria Grazia [1 ,2 ]
Naldini, Luigi [1 ,2 ]
机构：
[1] San Raffaele Telethon Inst Gene Therapy, San Rafael, CA USA
[2] Univ Vita Salute San Raffaele, Milan, Italy
[3] Ist Sci San Raffaele, San Rafael, CA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2008年 / 93卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2007.10.021
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：S16 / S16
页数：1
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