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- [21] A New Gene Therapy Approach to Treat Niemann-Pick Type C2 DiseaseMOLECULAR THERAPY, 2022, 30 (04) : 394 - 394Marco, Sara论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainSanchez, Xavier论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainElias, Gemma论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainRibera, Albert论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainSanchez, Victor论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainJoan, Bertolin论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainPerez, Jennifer论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainPerea, Marta论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainRoca, Carles论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainGarcia, Miquel论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainMolas, Maria论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainLeon, Xavier论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainMoliner, Manel论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainRuberte, Jesus论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Anim Hlth & Anat, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainHaurigot, Virginia论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainStorch, Judith论文数: 0 引用数: 0 h-index: 0机构: Rutgers State Univ, Dept Nutr Sci, New Brunswick, NJ USA Rutgers Ctr Lipid Res, New Brunswick, NJ USA Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, SpainBosch, Fatima论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Bellaterra, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Bellaterra, Spain
- [22] Respiratory disease in Niemann-Pick type C2 is caused by pulmonary alveolar proteinosisCLINICAL GENETICS, 2010, 77 (02) : 119 - 130Griese, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, Germany Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyBrasch, F.论文数: 0 引用数: 0 h-index: 0机构: Klinikum Bremen Mitte, Dept Pathol, Bremen, Germany Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyAldana, V. R.论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Mexico Dr Federico Gomez, Dept Pneumol & Resp Physiol, Mexico City, DF, Mexico Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyCabrera, M. M.论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Mexico Dr Federico Gomez, Dept Pathol, Mexico City, DF, Mexico Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyGoelnitz, U.论文数: 0 引用数: 0 h-index: 0机构: Univ Rostock, Albrecht Kossel Inst Neuroregenerat, Fac Med, Rostock, Germany Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyIkonen, E.论文数: 0 引用数: 0 h-index: 0机构: Univ Helsinki, Inst Biomed Anat, FIN-00014 Helsinki, Finland Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyKaram, B. J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Mexico Dr Federico Gomez, Dept Pneumol & Resp Physiol, Mexico City, DF, Mexico Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyLiebisch, G.论文数: 0 引用数: 0 h-index: 0机构: Klinikum Univ Regensburg, Inst Klin Chem, D-93053 Regensburg, Germany Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyLinder, M. D.论文数: 0 引用数: 0 h-index: 0机构: Univ Helsinki, Inst Biomed Anat, FIN-00014 Helsinki, Finland Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyLohse, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Munich, Dept Clin Chem, Munich, Germany Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyMeyer, W.论文数: 0 引用数: 0 h-index: 0机构: Queen Mary Univ London, St Bartholomews & Royal London Sch Med, London, England Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanySchmitz, G.论文数: 0 引用数: 0 h-index: 0机构: Klinikum Univ Regensburg, Inst Klin Chem, D-93053 Regensburg, Germany Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyPamir, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, Germany Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyRipper, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, Germany Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyRolfs, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Rostock, Albrecht Kossel Inst Neuroregenerat, Fac Med, Rostock, Germany Centogene GmbH, D-18057 Rostock, Germany Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanySchams, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, Germany Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, GermanyLezana, F. J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Mexico Dr Federico Gomez, Dept Pneumol & Resp Physiol, Mexico City, DF, Mexico Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, Germany
- [23] LIVER X RECEPTOR AGONISTS UP-REGULATE NIEMANN-PICK TYPE C1 AND NIEMANN-PICK TYPE C2 EXPRESSION IN apoE-/- MICECELL BIOLOGY INTERNATIONAL, 2008, 32 (03) : S18 - S18Tang, Chao Ke论文数: 0 引用数: 0 h-index: 0机构: Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R China Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R China论文数: 引用数: h-index:机构:Dai, Xiao Yan论文数: 0 引用数: 0 h-index: 0机构: Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R China Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R ChinaHao, Xin Rui论文数: 0 引用数: 0 h-index: 0机构: Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R China Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R ChinaCao, Dong Li论文数: 0 引用数: 0 h-index: 0机构: Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R China Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R ChinaHu, Yan Wei论文数: 0 引用数: 0 h-index: 0机构: Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R China Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R ChinaLi, Xiao Xu论文数: 0 引用数: 0 h-index: 0机构: Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R China Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R ChinaXiao, Ji论文数: 0 引用数: 0 h-index: 0机构: Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R China Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R ChinaLiu, Xie Hong论文数: 0 引用数: 0 h-index: 0机构: Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R China Univ S China, Inst Cardiovasc Res, Hengyang 421001, Hunan, Peoples R China
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