A Phase 2/3, Randomized, Double-Blind, Placebo-Controlled Study of Mitapivat in Patients with Sickle Cell Disease

被引：2
|
作者：
Howard, Joanna [1 ]
Kuo, Kevin H. M. [2 ]
Oluyadi, Abdulafeez [3 ]
Shao, Hui [3 ]
Morris, Susan [3 ]
Zaidi, Ahmar U. [3 ]
Van Beers, Eduard J. [4 ]
Thien, Swee Lay [5 ]
机构：
[1] Guys & St Thomas NHS Fdn Trust, Dept Hematol, London, England
[2] Univ Toronto, Div Med Oncol & Hematol, Toronto, ON, Canada
[3] Agios Pharmaceut Inc, Cambridge, MA USA
[4] Univ Med Ctr Utrecht, Creveldkliniek Dept Internal Med, Utrecht, Netherlands
[5] Natl Heart Lung & Blood Inst, Natl Inst Hlth, Sickle Cell Branch, Bethesda, MD USA
来源：
BLOOD | 2021年 / 138卷
关键词：
D O I：
10.1182/blood-2021-148370
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
3109
引用
收藏
页数：5
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