Comparison of the exon skipping efficacy of different chemically modified antisense oligonucleotides within the mouse retina

被引：0
|
作者：
Vazquez-Dominguez, I. [1 ,2 ]
Allo-Anido, A. [1 ]
Duijkers, L. [1 ]
Hoppenbrouwers, T. [1 ,2 ]
Hoogendoorn, A. [1 ]
Collin, R. W. J. [1 ,2 ]
Garanto, A. [1 ,3 ,4 ]
机构：
[1] Radboud Univ Nijmegen Med Ctr, Dept Human Genet, Nijmegen, Netherlands
[2] Radboud Univ Nijmegen Med Ctr, Donders Inst Brain Cognit & Behav, Nijmegen, Netherlands
[3] Radboud Univ Nijmegen Med Ctr, Dept Pediat, Amalia Childrens Hosp, Dept Human Genet, Nijmegen, Netherlands
[4] Radboud Univ Nijmegen Med Ctr, Radboud Inst Mol Life Sci RIMLS, Nijmegen, Netherlands
来源：
HUMAN GENE THERAPY | 2021年 / 32卷 / 19-20期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P338
引用
收藏
页码：A132 / A132
页数：1
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