Economic Impact of Immune Tolerance Induction (ITI) with Recombinant Factor VIII Fc Fusion Protein (rFVIIIFc) Compared to Conventional Recombinant Factor VIII (rFVIII)

被引:0
|
作者
Li, Nanxin [1 ]
Wilson, Koo [2 ]
Botteman, Marc [3 ]
Nicoloso, Daniel [3 ]
Krishnan, Sangeeta [1 ]
Su, Jun [1 ]
机构
[1] Bioverativ, Waltham, MA USA
[2] Swedish Orphan Biovitrum SOBI, Stockholm, Sweden
[3] Pharmerit Int, Bathesda, MD USA
关键词
D O I
10.1182/blood-2018-99-114993
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
3520
引用
收藏
页数:3
相关论文
共 50 条
  • [21] THE CLINICAL AND ECONOMIC IMPACT OF RECOMBINANT FACTOR VIII FC FUSION PROTEIN (RFVIIIFC) ON LONG-TERM JOINT HEALTH IN PEOPLE WITH HEMOPHILIA A (PWHA)
    Batt, K.
    Cockerham, A.
    Sacks, N.
    Jin, H.
    Nguyen, A. T. H.
    HAEMOPHILIA, 2022, 28 : 93 - 94
  • [22] POPULATION PHARMACOKINETIC MODEL FOR RECOMBINANT FACTOR VIII FC FUSION PROTEIN (RFVIIIFC) VALIDATED AND OPTIMIZED FOR USE IN CHILDREN
    Bukkems, L. H.
    Heijdra, J. M.
    Mathias, M.
    Collins, P. W.
    Hay, C. R. M.
    Leebeek, F. W. G.
    Meijer, K.
    Fijnvandraat, K.
    Chowdary, P.
    Cnossen, M. H.
    Mathot, R. A. A.
    HAEMATOLOGICA, 2019, 104 : 14 - 14
  • [23] Changing recombinant factor VIII to plasma-derived factor VIII during immune tolerance induction
    Dias, Maise Moreira
    Camelo, Ricardo Mesquita
    de Magalhaes, Laura Peixoto
    Jardim, Leticia Lemos
    de Oliveira, Andrea Goncalves
    de Albuquerque Ribeiro, Rosangela
    Franco, Vivian Karla Brognoli
    de Araujo Callado, Fabia Michelle Rodrigues
    Lorenzato, Claudia Santos
    Rezende, Suely Meireles
    PEDIATRIC HEMATOLOGY AND ONCOLOGY, 2024, 41 (01) : 74 - 80
  • [24] Long-term safety and efficacy of recombinant factor VIII Fc fusion protein (rFVIIIFc) in subjects with haemophilia A
    Nolan, B.
    Mahlangu, J.
    Perry, D.
    Young, G.
    Liesner, R.
    Konkle, B.
    Rangarajan, S.
    Brown, S.
    Hanabusa, H.
    Pasi, K. J.
    Pabinger, I.
    Jackson, S.
    Cristiano, L. M.
    Li, X.
    Pierce, G. F.
    Allen, G.
    HAEMOPHILIA, 2016, 22 (01) : 72 - 80
  • [25] Induction of immune tolerance with recombinant factor VIII in haemophilia A patients with inhibitors
    Batlle, J
    López, MF
    Brackmann, HH
    Gaillard, S
    Goudemand, J
    Humbert, J
    De Moerloose, P
    Maass, E
    Mauz-Körholz, C
    Sultan, Y
    Stieltjes, N
    HAEMOPHILIA, 1999, 5 (06) : 431 - 435
  • [26] Clotting and chromogenic factor VIII assay variability in post-infusion and spiked samples containing full-length recombinant FVIII or recombinant factor VIII Fc fusion protein (rFVIIIFc)
    Kitchen, Steve
    Jennings, Ian
    Makris, Mike
    Kitchen, Dianne Patricia
    Woods, Timothy A. L.
    Walker, Isobel D.
    INTERNATIONAL JOURNAL OF LABORATORY HEMATOLOGY, 2019, 41 (02) : 176 - 183
  • [27] Long-acting recombinant factor VIII Fc fusion protein (rFVIIIFc) for perioperative haemostatic management in severe haemophilia A
    Mahlangu, Johnny N.
    Ragni, Margaret
    Gupta, Naresh
    Rangarajan, Savita
    Klamroth, Robert
    Oldenburg, Johannes
    Nogami, Keiji
    Young, Guy
    Cristiano, Lynda M.
    Dong, Yingwen
    Allen, Geoffrey
    Pierce, Glenn F.
    Robinson, Brian
    THROMBOSIS AND HAEMOSTASIS, 2016, 116 (01) : 1 - 8
  • [28] USE OF RECOMBINANT FACTOR-VIII (RFVIII) FOR SURGERY
    ABILDGAARD, CF
    HARRISON, J
    HILGARTNER, M
    THROMBOSIS AND HAEMOSTASIS, 1991, 65 (06) : 706 - 706
  • [29] Recombinant Fusion Factor VIII-Fc Fusion Protein in Severe Haemophilia A Patients
    Le Quellec, Sandra
    HEMATOLOGIE, 2014, 20 (06): : 304 - 306
  • [30] Evaluation of the toxicology and pharmacokinetics of recombinant factor VIII Fc fusion protein in animals
    Dumont, Jennifer A.
    Loveday, Kenneth S.
    Light, David R.
    Pierce, Glenn F.
    Jiang, Haiyan
    THROMBOSIS RESEARCH, 2015, 136 (06) : 1266 - 1272