Gene therapy of murine GM1 gangliosidosis by genetically modified bone marrow hematopoietic progenitor cells.

被引：0
|
作者：
Sano, R [1 ]
Tessitore, A [1 ]
Mann, L [1 ]
d'Azzo, A [1 ]
机构：
[1] St Jude Childrens Res Hosp, Memphis, TN 38105 USA
来源：
AMERICAN JOURNAL OF HUMAN GENETICS | 2003年 / 73卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q3 [遗传学];
学科分类号：
071007 ; 090102 ;
摘要：
2693
引用
收藏
页码：627 / 627
页数：1
相关论文
共 50 条
  • [1] Gene therapy of murine GM1 gangliosidosis by genetically modified bone marrow hematopoietic progenitor cells
    Sano, R
    Tessitore, A
    Ingrassia, A
    d'Azzo, A
    MOLECULAR THERAPY, 2004, 9 : S265 - S265
  • [2] Functional amelioration of murine galactosialidosis by genetically modified bone marrow hematopoietic progenitor cells
    Leimig, T
    Mann, L
    Martin, MD
    Bonten, E
    Persons, D
    Knowles, J
    Allay, JA
    Cunningham, J
    Nienhuis, AW
    Smeyne, R
    d'Azzo, A
    BLOOD, 2002, 99 (09) : 3169 - 3178
  • [3] GENE-THERAPY IN GM1 GANGLIOSIDOSIS
    SEO, HC
    JOHNSON, PA
    PYRCE, D
    MASADA, RI
    KISHIMOTO, Y
    OBRIEN, JS
    FASEB JOURNAL, 1994, 8 (07): : A1440 - A1440
  • [4] BONE-MARROW TRANSPLANTATION IN CANINE GM1 GANGLIOSIDOSIS
    OBRIEN, JS
    STORB, R
    RAFF, RF
    HARDING, J
    APPELBAUM, F
    MORIMOTO, S
    KISHIMOTO, Y
    GRAHAM, T
    AHERNRINDELL, A
    OBRIEN, SL
    CLINICAL GENETICS, 1990, 38 (04) : 274 - 280
  • [5] Intracerebral cell transplantation therapy for murine GM1 gangliosidosis
    Sawada, Tomo
    Tanakaa, Akemi
    Higaki, Katsumi
    Takamura, Ayumi
    Nanba, Eiji
    Seto, Toshiyuki
    Maeda, Mitsuyo
    Yamaguchi, Etsuko
    Matsuda, Junichiro
    Yamano, Tunekazu
    BRAIN & DEVELOPMENT, 2009, 31 (10): : 717 - 724
  • [6] Intravenous Delivery of AAV Gene Therapy in GM1 Gangliosidosis
    Gross, Amanda L.
    Gray-Edwards, Heather
    Batista, Ana Rita
    Maitland, Stacy
    Sena-Esteves, Miguel
    Martin, Douglas R.
    MOLECULAR THERAPY, 2018, 26 (05) : 136 - 136
  • [7] Intravenous Delivery of AAV Gene Therapy in GM1 Gangliosidosis
    Gross, Amanda L.
    Gray-Edwards, Heather L.
    Bebout, Cassie N.
    Neilson, Kayly
    Brunson, Brandon L.
    Batista, Ana Rita
    Maitland, Stacy
    Sena-Esteves, Miguel
    Martin, Douglas
    MOLECULAR THERAPY, 2019, 27 (04) : 191 - 191
  • [8] Intravenous Delivery of AAV Gene Therapy in GM1 Gangliosidosis
    Gross, Amanda L.
    Gray-Edwards, Heather
    Sena-Esteves, Miguel
    Martin, Douglas R.
    MOLECULAR THERAPY, 2017, 25 (05) : 315 - 315
  • [9] Presymptomatic Gene Therapy Cures Feline GM1 Gangliosidosis
    McCurdy, Victoria J.
    Johnson, Aime K.
    Bradbury, Allison M.
    Randle, Ashley N.
    Gray-Edwards, Heather
    Hwang, Misako
    Leroy, Stanley G.
    Cox, Nancy R.
    Sena-Esteves, Miguel
    Martin, Douglas R.
    MOLECULAR THERAPY, 2012, 20 : S12 - S12
  • [10] Developement of an Ex Vivo Gene Therapy for Infantile GM1 Gangliosidosis
    Bucciarelli, Linda
    Fabris, Camilla
    Milazzo, Rita
    Biffi, Alessandra
    Poletti, Valentina
    MOLECULAR THERAPY, 2023, 31 (04) : 38 - 39
12345