CRISPR/CAS9 BASED GENE EDITING OF CFTR DEEP INTRONIC MUTATIONS

被引:0
|
作者
Sanz, D. J. [1 ]
Hollywood, J. A. [2 ]
Harrison, P. [1 ]
机构
[1] Univ Coll Cork, Physiol, Cork, Ireland
[2] Univ Auckland, Sch Med, Auckland, New Zealand
关键词
D O I
暂无
中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
195
引用
收藏
页码:265 / 266
页数:2
相关论文
共 50 条
  • [41] Combining CRISPR/Cas9 and rAAV Templates for Efficient Gene Editing
    Kaulich, Manuel
    Dowdy, Steven F.
    NUCLEIC ACID THERAPEUTICS, 2015, 25 (06) : 287 - 296
  • [42] Alzheimer disease mice improve with CRISPR–Cas9 gene editing
    Ian Fyfe
    Nature Reviews Neurology, 2019, 15 : 247 - 247
  • [43] Gene Editing of the AAVS1 Locus with CRISPR/Cas9
    Vieira, Mathieu
    Bello, Ana Buj
    Le Roy, Florence G.
    MOLECULAR THERAPY, 2015, 23 : S53 - S53
  • [44] A CRISPR/Cas9 system adapted for gene editing in marine algae
    Nymark, Marianne
    Sharma, Amit Kumar
    Sparstad, Torfinn
    Bones, Atle M.
    Winge, Per
    SCIENTIFIC REPORTS, 2016, 6
  • [45] Editing plant genomes with CRISPR/Cas9
    Belhaj, Khaoula
    Chaparro-Garcia, Angela
    Kamoun, Sophien
    Patron, Nicola J.
    Nekrasov, Vladimir
    CURRENT OPINION IN BIOTECHNOLOGY, 2015, 32 : 76 - 84
  • [46] Off-target effects in CRISPR/Cas9 gene editing
    Guo, Congting
    Ma, Xiaoteng
    Gao, Fei
    Guo, Yuxuan
    FRONTIERS IN BIOENGINEERING AND BIOTECHNOLOGY, 2023, 11
  • [47] Somatic Gene Therapy of Mucopolysaccharidosis with CRISPR/Cas9 Genome Editing
    Kao, Winston W. Y.
    Ferreira, Tarsis
    Dong, Fei
    Hu, Yueh-Chiang
    Call, Mindy Kay
    Coulson-Thomas, Vivien Jane
    Zhang, Jianhua
    Rice, Taylor
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2016, 57 (12)
  • [48] A CRISPR/Cas9 system adapted for gene editing in marine algae
    Marianne Nymark
    Amit Kumar Sharma
    Torfinn Sparstad
    Atle M. Bones
    Per Winge
    Scientific Reports, 6
  • [49] Gene Editing With CRISPR/Cas9 RNA-Directed Nuclease
    Doetschman, Thomas
    Georgieva, Teodora
    CIRCULATION RESEARCH, 2017, 120 (05) : 876 - 894
  • [50] CRISPR/Cas9 mediated editing of phytoene desaturase gene in squash
    Thakur, Shallu
    Meru, Geoffrey
    JOURNAL OF PLANT BIOCHEMISTRY AND BIOTECHNOLOGY, 2023, 32 (04) : 862 - 869