Outcome measures for Duchenne muscular dystrophy from ambulant to non-ambulant: Implications for clinical trials

被引：0
|
作者：
Domingos, J. [1 ]
Eagle, M. [2 ]
Moraux, A. [3 ]
Butler, J. [1 ]
Decostre, V. [3 ]
Ridout, D. [4 ]
Mayhew, A. [2 ]
Selby, V. [1 ]
Guglieri, M. [2 ]
Van der Holst, M. [5 ]
Jansen, M. [6 ]
Verschuuren, J. [5 ]
de Groot, I. [6 ]
Niks, E. [5 ]
Servais, L. [3 ]
Hogrel, J. Y. [3 ]
Straub, V. [2 ]
Voit, T. [7 ]
Ricotti, V. [1 ]
Muntoni, F. [1 ]
机构：
[1] UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
[2] Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, England
[3] Grp Hosp Pitie Salpetriere, Inst Myol, Paris, France
[4] UCL Inst Child Hlth, Populat Policy & Practice Programme, London, England
[5] Leiden Univ, Med Ctr, Leiden, Netherlands
[6] Radboud Univ Nijmegen, Med Ctr, Nijmegen, Netherlands
[7] UCL Inst Child Hlth, Biomed Res Ctr, London, England
来源：
NEUROMUSCULAR DISORDERS | 2016年 / 26卷
关键词：
D O I：
10.1016/j.nmd.2016.06.358
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
P.329
引用
收藏
页码：S185 / S185
页数：1
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