Targeting ATXN2 Using Antisense Oligonucleotides as a Treatment for Spinocerebellar Ataxia Type 2 (SCA2)

被引：0
|
作者：
Scoles, Daniel [4 ]
Schneider, Matthew [4 ]
Meera, Pratap [3 ]
Figueroa, Karla [4 ]
Hung, Gene [1 ]
Rigo, Frank [2 ]
Bennett, Frank [2 ]
Otis, Thomas [3 ]
Pulst, Stefan [4 ]
机构：
[1] ISIS Pharmaceut, 2280 Faraday Ave, Carlsbad, CA 92008 USA
[2] Isis Pharmaceut Inc, Carlsbad, CA USA
[3] Univ Calif Los Angeles, Los Angeles, CA USA
[4] Univ Utah, Salt Lake City, UT USA
来源：
NEUROLOGY | 2016年 / 86卷
关键词：
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
S30.007
引用
收藏
页数：2
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