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- [21] Correction of Glycogen Storage Disease Type III with an AAV Vector Encoding a Bacterial Glycogen Debranching EnzymeMOLECULAR THERAPY, 2019, 27 (04) : 17 - 17Lim, Jeong-A论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Pediat Med Genet, Durham, NC USA Duke Univ, Sch Med, Pediat Med Genet, Durham, NC USAChoi, Su Jin论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Pediat Med Genet, Durham, NC USA Duke Univ, Sch Med, Pediat Med Genet, Durham, NC USAGao, Fengqin论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Pediat Med Genet, Durham, NC USA Duke Univ, Sch Med, Pediat Med Genet, Durham, NC USAKishnani, Priya论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Pediat Med Genet, Durham, NC USA Duke Univ, Sch Med, Pediat Med Genet, Durham, NC USASun, Baodong论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Pediat Med Genet, Durham, NC USA Duke Univ, Sch Med, Pediat Med Genet, Durham, NC USA
- [22] Adeno-Associated Virus Gene Therapy Prevents Hepatocellular Adenoma in Murine Model of Glycogen Storage Disease Type IaHEPATOLOGY, 2012, 56 (05) : 1593 - 1595Wang, Lili论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA
- [23] Pathogenesis of Growth Failure in Murine and Canine Glycogen Storage Disease-Ia and Partial Reversal of Growth Failure Using Adeno-Associated Viral Vector TherapyMOLECULAR THERAPY, 2013, 21 : S105 - S106Brooks, Elizabeth J.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Durham, NC USA Duke Univ, Med Ctr, Durham, NC USALittle, Dianne论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Durham, NC USA Duke Univ, Med Ctr, Durham, NC USAArumugam, Ramamani论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Durham, NC USA Duke Univ, Med Ctr, Durham, NC USASun, Baodong论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Durham, NC USA Duke Univ, Med Ctr, Durham, NC USACurtis, Sarah论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Durham, NC USA Rehoboth Beach Anim Hosp, Rehoboth Beach, DE USA Duke Univ, Med Ctr, Durham, NC USADeMaster, Amanda论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Durham, NC USA East Lincoln Anim Hosp, Denver, NC USA Duke Univ, Med Ctr, Durham, NC USAMaranzano, Michael论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Durham, NC USA Duke Univ, Med Ctr, Durham, NC USAJackson, Mark W.论文数: 0 引用数: 0 h-index: 0机构: Univ Glasgow, Glasgow, Lanark, Scotland Duke Univ, Med Ctr, Durham, NC USA论文数: 引用数: h-index:机构:Freemark, Michael S.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Durham, NC USA Duke Univ, Med Ctr, Durham, NC USAKoeberl, Dwight D.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Durham, NC USA Duke Univ, Med Ctr, Durham, NC USA
- [24] Kinetics of Transgene Expression in the Liver Following Transduction of Neonatal Mice with a Non-Primate Lentiviral Vector Indicates Selective Growth Advantage of Transduced HepatocytesHUMAN GENE THERAPY, 2009, 20 (05) : 545 - 546Simerzin, A.论文数: 0 引用数: 0 h-index: 0机构: Hadassah Univ Hosp, Goldyne Savad Inst Gene Therapy, IL-91120 Jerusalem, Israel Univ London Imperial Coll Sci Technol & Med, Gene Therapy Grp, London SW7 2AZ, EnglandCondiotti, R.论文数: 0 引用数: 0 h-index: 0机构: Hadassah Univ Hosp, Goldyne Savad Inst Gene Therapy, IL-91120 Jerusalem, Israel Univ London Imperial Coll Sci Technol & Med, Gene Therapy Grp, London SW7 2AZ, EnglandThemis, M.论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, Gene Therapy Grp, London SW7 2AZ, England Univ London Imperial Coll Sci Technol & Med, Gene Therapy Grp, London SW7 2AZ, EnglandWaddington, S. N.论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, Gene Therapy Grp, London SW7 2AZ, England Univ London Imperial Coll Sci Technol & Med, Gene Therapy Grp, London SW7 2AZ, EnglandGalun, E.论文数: 0 引用数: 0 h-index: 0机构: Hadassah Univ Hosp, Goldyne Savad Inst Gene Therapy, IL-91120 Jerusalem, Israel Univ London Imperial Coll Sci Technol & Med, Gene Therapy Grp, London SW7 2AZ, England
- [25] Hepatorenal Correction in Murine Glycogen Storage Disease Type I With a Double-stranded Adeno-associated Virus VectorMOLECULAR THERAPY, 2011, 19 (11) : 1961 - 1970Luo, Xiaoyan论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USA Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USAHall, Gentzon论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Dept Med, Durham, NC USA Ctr Human Genet, Div Nephrol, Durham, NC USA Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USALi, Songtao论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USA Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USABird, Andrew论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USA Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USALavin, Peter J.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Dept Med, Durham, NC USA Ctr Human Genet, Div Nephrol, Durham, NC USA Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USAWinn, Michelle P.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Dept Med, Durham, NC USA Ctr Human Genet, Div Nephrol, Durham, NC USA Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USAKemper, Alex R.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Program Pediat Hlth Serv Res, Dept Pediat, Durham, NC 27710 USA Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USABrown, Talmage T.论文数: 0 引用数: 0 h-index: 0机构: N Carolina State Univ, Coll Vet Med, Raleigh, NC USA Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USAKoeberl, Dwight D.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USA Duke Univ, Med Ctr, Div Med Genet, Dept Pediat, Durham, NC 27710 USA
- [26] Glycogen Storage Disease Type Ia in Canines: A Model for Human Metabolic and Genetic Liver DiseaseJOURNAL OF BIOMEDICINE AND BIOTECHNOLOGY, 2011,Specht, Andrew论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Small Anim Clin Sci, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USAFiske, Laurie论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Div Pediat Endocrinol, Dept Pediat, Glycogen Storage Dis Program, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USAErger, Kirsten论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USACossette, Travis论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USAVerstegen, John论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Large Anim Clin Sci, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USACampbell-Thompson, Martha论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Pathol Immunol & Lab Med, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USAStruck, Maggie B.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Anim Care Serv, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USALee, Young Mok论文数: 0 引用数: 0 h-index: 0机构: NICHHD, Sect Cellular Differentiat, PDEGEN, NIH, Bethesda, MD 20892 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USAChou, Janice Y.论文数: 0 引用数: 0 h-index: 0机构: NICHHD, Sect Cellular Differentiat, PDEGEN, NIH, Bethesda, MD 20892 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USAByrne, Barry J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Div Cellular & Mol Therapy, Dept Pediat, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USACorreia, Catherine E.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Div Pediat Endocrinol, Dept Pediat, Glycogen Storage Dis Program, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USAMah, Cathryn S.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Div Cellular & Mol Therapy, Dept Pediat, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USAWeinstein, David A.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Div Pediat Endocrinol, Dept Pediat, Glycogen Storage Dis Program, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USAConlon, Thomas J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Dept Pediat, Coll Med, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA
- [27] Correction of Murine Sickle Cell Disease Using Non-Ablative Conditioning and Autologous Bone Marrow Cells Transduced with a Gamma Globin Lentiviral VectorMOLECULAR THERAPY, 2013, 21 : S163 - S163Pestina, Tamara I.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Memphis, TN 38105 USAHargrove, Phillip W.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Memphis, TN 38105 USAZhao, Hui Fen论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Memphis, TN 38105 USAPersons, Derek A.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Memphis, TN 38105 USA
- [28] Inhibition of Wnt/β-catenin signaling reduces renal fibrosis in murine glycogen storage disease type IaBIOCHIMICA ET BIOPHYSICA ACTA-MOLECULAR BASIS OF DISEASE, 2024, 1870 (01):Lee, Cheol论文数: 0 引用数: 0 h-index: 0机构: Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USA Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USAPratap, Kunal论文数: 0 引用数: 0 h-index: 0机构: Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USA Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USAZhang, Lisa论文数: 0 引用数: 0 h-index: 0机构: Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USA Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USAChen, Hung Dar论文数: 0 引用数: 0 h-index: 0机构: Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USA Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USAGautam, Sudeep论文数: 0 引用数: 0 h-index: 0机构: Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USA Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USAArnaoutova, Irina论文数: 0 引用数: 0 h-index: 0机构: Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USA Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USARaghavankutty, Mahadevan论文数: 0 引用数: 0 h-index: 0机构: Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Dev Genet, Div Translat Med, NIH, Bethesda, MD 20802 USA Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USAStarost, Matthew F.论文数: 0 引用数: 0 h-index: 0机构: NIH, Div Vet Resources, Bethesda, MD 20892 USA Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USAKahn, Michael论文数: 0 引用数: 0 h-index: 0机构: City Hope Natl Med Ctr, Dept Canc Biol & Mol Med, Beckman Res Inst, Duarte, CA 91010 USA Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USAMansfield, Brian C.论文数: 0 引用数: 0 h-index: 0机构: Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USA Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USAChou, Janice Y.论文数: 0 引用数: 0 h-index: 0机构: Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USA NIH, Bldg 10,Room 8N-240C,10 Ctr Dr, Bethesda, MD 20892 USA Eunice Kennedy Shriver Natl Inst Child Hlth & Huma, Sect Cellular Differentiat, Div Translat Med, NIH, Bethesda, MD 20802 USA
- [29] Correction of osteopetrosis in the neonate oc/oc murine model after lentiviral vector gene therapy and non-genotoxic conditioningFRONTIERS IN ENDOCRINOLOGY, 2024, 15Penna, Sara论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyZecchillo, Alessandra论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy Univ Milano Bicocca, Translat & Mol Med DIMET, Milan, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyDi Verniere, Martina论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyFontana, Elena论文数: 0 引用数: 0 h-index: 0机构: CNR, Ist Ric Genet & Biomed, Milan Unit, Milan, Italy Human Res Hosp IRCCS, Rozzano, MI, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyIannello, Valeria论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyPalagano, Eleonora论文数: 0 引用数: 0 h-index: 0机构: Human Res Hosp IRCCS, Rozzano, MI, Italy CNR, Ist Biosci & Biorisorse, Florence Unit, Sesto Fiorentino, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyMantero, Stefano论文数: 0 引用数: 0 h-index: 0机构: CNR, Ist Ric Genet & Biomed, Milan Unit, Milan, Italy Human Res Hosp IRCCS, Rozzano, MI, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyCappelleri, Andrea论文数: 0 引用数: 0 h-index: 0机构: UniMi Fdn, Mouse & Anim Pathol Lab, Milan, Italy Univ Milan, Dept Vet Med & Anim Sci, Lodi, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyRizzoli, Elena论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalySanti, Ludovica论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyCrisafulli, Laura论文数: 0 引用数: 0 h-index: 0机构: CNR, Ist Ric Genet & Biomed, Milan Unit, Milan, Italy Human Res Hosp IRCCS, Rozzano, MI, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyFilibian, Marta论文数: 0 引用数: 0 h-index: 0机构: Univ Pavia, Ctr Grandi Strumenti, Biomed Imaging Lab, Pavia, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy论文数: 引用数: h-index:机构:Basso-Ricci, Luca论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyScala, Serena论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyScanziani, Eugenio论文数: 0 引用数: 0 h-index: 0机构: UniMi Fdn, Mouse & Anim Pathol Lab, Milan, Italy Univ Milan, Dept Vet Med & Anim Sci, Lodi, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalySchinke, Thorsten论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Dept Osteol & Biomech, Hamburg, Germany IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyFicara, Francesca论文数: 0 引用数: 0 h-index: 0机构: CNR, Ist Ric Genet & Biomed, Milan Unit, Milan, Italy Human Res Hosp IRCCS, Rozzano, MI, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalySobacchi, Cristina论文数: 0 引用数: 0 h-index: 0机构: CNR, Ist Ric Genet & Biomed, Milan Unit, Milan, Italy Human Res Hosp IRCCS, Rozzano, MI, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyVilla, Anna论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy CNR, Ist Ric Genet & Biomed, Milan Unit, Milan, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyCapo, Valentina论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy CNR, Ist Ric Genet & Biomed, Milan Unit, Milan, Italy IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy
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