2.5-years of vamorolone treatment in Duchenne muscular dystrophy: Results of an open label long-term extension

被引：1
|
作者：
Hoffman, E. [1 ]
Dang, U. [1 ]
Clemens, P. [2 ]
Gordish-Dressman, H. [3 ]
Schwartz, B. [4 ]
Mengle-Gaw, L. [4 ]
Leinonen, M. [5 ]
Smith, E. [6 ]
Castro, D. [7 ]
Kuntz, N. [8 ]
Finkel, R. [9 ]
Tulinius, M. [10 ]
Nevo, Y. [11 ]
Ryan, M. [12 ]
Webster, R. [13 ]
van den Anker, J. [3 ]
Ward, L. [14 ]
Damsker, J. [15 ]
McDonald, C. [16 ]
Guglieri, M. [17 ]
Mah, J. [18 ]
机构：
[1] SUNY Binghamton, Binghamton, NY USA
[2] Univ Pittsburgh, Pittsburgh, PA USA
[3] Childrens Natl Med Ctr, Washington, DC 20010 USA
[4] Camden Associates, St Louis, MO USA
[5] Santhera, Pratteln, Switzerland
[6] Duke Univ, Chapel Hill, NC USA
[7] UTSW, Dallas, TX USA
[8] Luries Childrens Hosp, Chicago, IL USA
[9] Nemours Childrens Hosp, Orlando, FL USA
[10] Queen Silvia Childrens Hosp, Gothenburg, Sweden
[11] Tel Aviv Univ, Tel Aviv, Israel
[12] Royal Childrens Hosp, Melbourne, Vic, Australia
[13] Childrens Hosp Westmead, Sydney, NSW, Australia
[14] Childrens Hosp Eastern Ontario, Ottawa, ON, Canada
[15] ReveraGen, Rockville, MD USA
[16] Univ Calif Davis, Davis, CA 95616 USA
[17] Univ Newcastle, Newcastle, England
[18] Alberta Childrens Prov Gen Hosp, Calgary, AB, Canada
来源：
NEUROMUSCULAR DISORDERS | 2021年 / 31卷
关键词：
D O I：
10.1016/j.nmd.2021.07.020
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
O.3a
引用
收藏
页码：S48 / S48
页数：1
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