SGT-001 Micro-dystrophin gene therapy for Duchenne muscular dystrophy

被引：3
|
作者：
Schneider, J. [1 ]
Gonzalez, J. [1 ]
Brown, K. [1 ]
Golebiowski, D. [1 ]
Ricotti, V. [1 ]
Quiroz, J. [1 ]
Morris, C. [1 ]
机构：
[1] Solid Biosci, Cambridge, MA USA
来源：
NEUROMUSCULAR DISORDERS | 2017年 / 27卷
关键词：
D O I：
10.1016/j.nmd.2017.06.343
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
P.303
引用
收藏
页码：S188 / S188
页数：1
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