LONGTERM TREATMENT EFFECTS OF INOTERSEN ON QUALITY OF LIFE IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHY

被引:0
|
作者
Brown, Duncan
Karam, Chafic
Yang, Min
Done, Nicolae
Zhu, JingJing
Greatsinger, Ali
Bozas, Ana
Llonch, Montserrat Vera
Signorovitch, James
机构
关键词
D O I
暂无
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
105
引用
收藏
页码:S57 / S57
页数:1
相关论文
共 50 条
  • [31] Indirect treatment comparison (ITC) of the efficacy of vutrisiran and tafamidis for hereditary transthyretin-mediated amyloidosis with polyneuropathy
    Merkel, Madeline
    Danese, David
    Chen, Chongshu
    Wang, Jessie
    Wu, Aozhou
    Yang, Hongbo
    Lin, Hollis
    EXPERT OPINION ON PHARMACOTHERAPY, 2023, 24 (10) : 1205 - 1214
  • [32] Long-term Integrated Safety of Patisiran in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy
    Gillmore, Julian
    Berk, John
    Dispenzieri, Angela
    Polydefkis, Michael
    Gonzalez-Duarte, Alejandra
    Sekijima, Yoshiki
    Sweetser, Marianne T.
    Arum, Seth
    Wang, Jing Jing
    White, Matthew T.
    Maurer, Mathew
    JOURNAL OF CARDIAC FAILURE, 2020, 26 (10) : S67 - S68
  • [33] IDENTIFYING MIXED PHENOTYPE: EVALUATING THE PRESENCE OF POLYNEUROPATHY IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH CARDIOMYOPATHY
    Grogan, Martha
    Hawkins, Philip
    Kristen, Arnt
    Berk, John
    Suhr, Ole B.
    Lin, Hollis
    Merkel, Madeline
    McManus, Anastasia
    Powell, Christine
    Vest, John
    Karsten, Verena
    Judge, Daniel
    MUSCLE & NERVE, 2020, 62 : S107 - S107
  • [34] Identifying Mixed Phenotype: Evaluating the Presence of Polyneuropathy in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Cardiomyopathy
    Merkel, Madeline
    Grogan, Martha
    Hawkins, Philip N.
    Kristen, Arnt V.
    Berk, John L.
    Suhr, Ole B.
    Lin, Hollis
    McManus, Anastasia
    Powell, Christine
    Vest, John
    Karsten, Verena
    Judge, Daniel P.
    NEUROLOGY, 2020, 94 (15)
  • [35] Efficacy and safety of vutrisiran for patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: a randomized clinical trial
    Adams, David
    Tournev, Ivailo L.
    Taylor, Mark S.
    Coelho, Teresa
    Plante-Bordeneuve, Violaine
    Berk, John L.
    Gonzalez-Duarte, Alejandra
    Gillmore, Julian D.
    Low, Soon-Chai
    Sekijima, Yoshiki
    Obici, Laura
    Chen, Chongshu
    Badri, Prajakta
    Arum, Seth M.
    Vest, John
    Polydefkis, Michael
    AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2023, 30 (01): : 18 - 26
  • [36] Long-term integrated safety of patisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy
    Gillmore, J.
    Berk, J.
    Dispenzieri, A.
    Polydefkis, M.
    Gonzalez-Duarte, A.
    Sekijima, Y.
    Sweetser, M. T.
    Arum, S.
    Wang, J. J.
    White, M. T.
    Maurer, M.
    EUROPEAN HEART JOURNAL, 2020, 41 : 2129 - 2129
  • [37] Safety and efficacy of inotersen in patients with hereditary transthyretin amyloidosis with polyneuropathy (NEURO-TTR)
    Gertz, Morie
    Wang, Annabel
    Coelho, Teresa
    Cruz, Marcia Waddington
    Polydefkis, Michael
    Dyck, Peter
    Scheinberg, Morton
    Plante-Bordeneuve, Violaine
    Berk, John
    Barroso, Fabio
    Brannagan, Thomas
    Khella, Sami
    Conceicao, Isabel
    Gorevic, Peter
    Monia, Brett
    Benson, Merrill
    JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2018, 23 (04) : 399 - 400
  • [38] Responsiveness of mNIS+7 components in inotersen treatment of hereditary transthyretin amyloidosis polyneuropathy
    Dyck, P. J. B.
    Kincaid, J. C.
    Wiesman, J. F.
    Polydefkis, M.
    Litchy, W. J.
    Mauermann, M. L.
    Ackermann, E. J.
    Guthrie, S.
    Pollock, M.
    Jung, S. W.
    Baker, B. F.
    Dyck, P. J.
    EUROPEAN JOURNAL OF NEUROLOGY, 2019, 26 : 714 - 714
  • [39] Efficacy and Safety With >3 Years of Inotersen Treatment for the Polyneuropathy of Hereditary Transthyretin Amyloidosis
    Coelho, M.
    Whelan, C.
    Conceicao, I.
    Brannagan, T., III
    Wang, A.
    Polydefkis, M.
    Dyck, P.
    Plante-Bordeneuve, V.
    Berk, J.
    Merlini, G.
    Obici, L.
    Drachman, B.
    Gorevic, P.
    Schmidt, H.
    Campistol Plana, J.
    Gamez, J.
    Kristen, A.
    Mazzeo, A.
    Narayana, A.
    Olugemo, K.
    Aquino, P.
    Benson, M.
    Gertz, M.
    EUROPEAN JOURNAL OF NEUROLOGY, 2021, 28 : 71 - 71
  • [40] Patisiran, an RNAi therapeutic for the treatment of hereditary transthyretin-mediated amyloidosis
    Kristen, Arnt, V
    Ajroud-Driss, Senda
    Conceicao, Isabel
    Gorevic, Peter
    Kyriakides, Theodoros
    Obici, Laura
    NEURODEGENERATIVE DISEASE MANAGEMENT, 2019, 9 (01) : 5 - 24