The Roche HD natural history study - An external comparator by design

被引:0
|
作者
Hooper, G. [1 ]
Palermo, G. [2 ]
Hlavac, F. [3 ]
Finnegan, C. [4 ]
Frick, E. [5 ]
Boak, L. [6 ]
Doody, R. [7 ,8 ]
Schobel, S. [6 ]
Leavitt, B. [9 ]
机构
[1] Roche Prod Ltd, Neurosci Huntingtons Dis, Welwyn Garden City, Herts, England
[2] F Hoffmann La Roche Ltd, Prod Dev, Basel, Switzerland
[3] F Hoffmann La Roche Ltd, Prod Dev Global, Basel, Switzerland
[4] Almac Grp, Almac Clin Technol LLC, Souderton, PA USA
[5] F Hoffmann La Roche Ltd, PD Clin Operat, Basel, Switzerland
[6] F Hoffmann La Roche Ltd, Prod Dev Neurosci, Basel, Switzerland
[7] F Hoffmann La Roche Ltd, Basel, Switzerland
[8] Genentech Inc, Neurodegenerat, San Francisco, CA 94080 USA
[9] Univ British Columbia, Dept Med Genet, Ctr Mol Med & Therapeut, Vancouver, BC, Canada
关键词
D O I
10.1016/j.jns.2019.10.1409
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
WCN19-1911
引用
收藏
页数:1
相关论文
共 50 条
  • [31] New Methodologies in the Study of Natural History
    Polcha, Elizabeth
    EARLY AMERICAN LITERATURE, 2021, 56 (02) : 545 - 557
  • [32] A Study of the Natural History of Pachyonychia Congenita
    Paller, Amy S.
    Shah, Sonal
    Kenner-Bell, Brandi
    PEDIATRIC DERMATOLOGY, 2010, 27 (05) : 567 - 567
  • [33] A natural history study of hexosaminidase deficiency
    Bjoraker, Kendra
    Eisengart, Julie
    Karachunski, Peter
    Oz, Gulin
    Whitley, Chester
    MOLECULAR GENETICS AND METABOLISM, 2010, 99 (02) : S11 - S11
  • [34] NATURAL HISTORY STUDY OF SORD NEUROPATHY
    Cortese, Andrea
    Dohrn, Maike
    Curro, Riccardo
    Seeman, Pavel
    Stojkovic, Tanya
    Hammans, Simon
    Previtali, Stefano
    Bolino, Alessandra
    Schenone, Angelo
    Kennerson, Marina
    Rojas-Garcia, Ricardo
    Sevilla, Teresa
    Hahn, Katrin
    Claeys, Kristl
    Brunkhorst, Robert
    Cavalcanti, Francesca
    Manganelli, Fiore
    Zhang, Ruxu
    Houlden, Henry
    Scherer, Steven
    Herrmann, David
    Pareyson, Davide
    Reilly, Mary
    Shy, Michael
    Zuchner, Stephan
    JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2022, 27 : S28 - S28
  • [35] A natural history study of hexosaminidase deficiency
    Bjoraker, Kendra J.
    Whitley, Chester B.
    Lawrence, Charnas
    MOLECULAR GENETICS AND METABOLISM, 2009, 96 (02) : S15 - S15
  • [36] The natural history of the news: An epigenetic study
    Hamilton, John Maxwell
    Tworek, Heidi J. S.
    JOURNALISM, 2017, 18 (04) : 391 - 407
  • [37] + STUDY OF NATURAL HISTORY OF IDIOPATHIC PROCTITIS
    JONES, JEL
    WILSON, CWE
    JONES, FA
    COOPER, GW
    NEWELL, AC
    GASTROENTEROLOGY, 1963, 44 (06) : 835 - &
  • [38] A STUDY OF THE NATURAL-HISTORY OF EAU
    BLOOM, JN
    NI, M
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 1992, 33 (04) : 932 - 932
  • [39] Why Study the History of the Natural Sciences?
    Martin, Joseph D.
    HISTORICAL STUDIES IN THE NATURAL SCIENCES, 2024, 54 (01) : 1 - 2
  • [40] Study design and baseline findings from the progression of ocular findings (PROOF) natural history study of dry eye
    Peter J. McDonnell
    Stephen C. Pflugfelder
    Michael E. Stern
    David R. Hardten
    Taryn Conway
    Linda Villanueva
    David A. Hollander
    BMC Ophthalmology, 17