AAV9 gene therapy rescues a murine model of Menkes disease

被引：0
|
作者：
Kaler, Stephen G. [1 ]
Donsante, Anthony [1 ]
Haddad, Marie-Reine [1 ]
机构：
[1] NICHD, Program Mol Med, NIH, Bethesda, MD USA
来源：
HUMAN GENE THERAPY | 2011年 / 22卷 / 10期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
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页码：A77 / A78
页数：2
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