First in man: gene editing for the treatment of transthyretin amyloidosis

被引:0
|
作者
Liuzzo, Giovanna [1 ]
Patrono, Carlo [2 ]
机构
[1] Catholic Univ, Sch Med, Fdn Policlin Univ A Gemelli IRCCS, Dept Cardiovasc & Pulm Sci, Largo A Gemelli 8, I-00168 Rome, Italy
[2] Catholic Univ, Sch Med, Fdn Policlin Univ A Gemelli IRCCS, Dept Pharmacol, Largo A Gemelli 8, I-00168 Rome, Italy
关键词
D O I
10.1093/eurheartj/ehab542
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
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页码:3597 / 3598
页数:2
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