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- [33] INTERNATIONAL, MULTI-CENTER, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED PHASE 3 STUDY ASSESSING IN PARALLEL GROUPS THE EFFICACY AND SAFETY OF 2 DOSES OF PXT3003 IN PATIENTS WITH CHARCOT-MARIE-TOOTH DISEASE TYPE 1A TREATED FOR 15 MONTHS JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2016, 21 (03) : 234 - 234