Patient Advocacy Leadership in Advancing Clinical Recommendations in Ultra-Rare Disease: The CLN1 Batten Disease Experience

被引：0
|
作者：
King, S.
Frazier, M.
机构：
来源：
ANNALS OF NEUROLOGY | 2019年 / 86卷
关键词：
Rare Diseases;
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
215
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页码：S139 / S139
页数：1
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