Results from First-in-Human Clinical Trial of RP-A501 (AAV9:LAMP2B) Gene Therapy Treatment for Danon Disease

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作者
Greenberg, Barry
Eshraghian, Emily
Battiprolu, Pavan
Ricks, David
Yarabe, Paul
Schwartz, Jonathan
Patel, Kinnari
Shah, Guarav
Trevejo, Jose
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R5 [内科学];
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1002 ; 100201 ;
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A10727
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页数:2
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