Results from First-in-Human Clinical Trial of RP-A501 (AAV9:LAMP2B) Gene Therapy Treatment for Danon Disease

被引：0
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作者：
Greenberg, Barry
Eshraghian, Emily
Battiprolu, Pavan
Ricks, David
Yarabe, Paul
Schwartz, Jonathan
Patel, Kinnari
Shah, Guarav
Trevejo, Jose
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来源：
CIRCULATION | 2021年 / 144卷
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暂无
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R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
A10727
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页数：2
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