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- [21] Reprogramming Adeno-Associated Virus Tropism via Displayed Peptides Tiling Receptor-Ligands in Mice and Non-Human PrimatesMOLECULAR THERAPY, 2024, 32 (04) : 167 - 168Portell, Andrew论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Bioengn, La Jolla, CA USA Univ Calif San Diego, Bioengn, La Jolla, CA USAFord, Kyle论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Bioengn, La Jolla, CA USA Univ Calif San Diego, Bioengn, La Jolla, CA USADuy An Le论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Bioengn, La Jolla, CA USA Univ Calif San Diego, Bioengn, La Jolla, CA USATarantal, Alice F.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Davis, CA USA Univ Calif San Diego, Bioengn, La Jolla, CA USAMali, Prashant论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Bioengn, La Jolla, CA USA Univ Calif San Diego, Bioengn, La Jolla, CA USA
- [22] Adeno-associated virus type 6 is retrogradely transported in the non-human primate brainGene Therapy, 2013, 20 : 1178 - 1183W San Sebastian论文数: 0 引用数: 0 h-index: 0机构: University of California San Francisco,Department of Neurological SurgeryL Samaranch论文数: 0 引用数: 0 h-index: 0机构: University of California San Francisco,Department of Neurological SurgeryG Heller论文数: 0 引用数: 0 h-index: 0机构: University of California San Francisco,Department of Neurological SurgeryA P Kells论文数: 0 引用数: 0 h-index: 0机构: University of California San Francisco,Department of Neurological SurgeryJ Bringas论文数: 0 引用数: 0 h-index: 0机构: University of California San Francisco,Department of Neurological SurgeryP Pivirotto论文数: 0 引用数: 0 h-index: 0机构: University of California San Francisco,Department of Neurological SurgeryJ Forsayeth论文数: 0 引用数: 0 h-index: 0机构: University of California San Francisco,Department of Neurological SurgeryK S Bankiewicz论文数: 0 引用数: 0 h-index: 0机构: University of California San Francisco,Department of Neurological Surgery
- [23] Comparison of Adeno-Associated Viral Capsids for Gene Transfer into Non-Human Primate LiverMOLECULAR THERAPY, 2022, 30 (04) : 249 - 249Berthelette, Patricia论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Genom Med Unit, Framingham, MA USA Sanofi, Genom Med Unit, Framingham, MA USAYu, Dan论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Genom Med Unit, Framingham, MA USA Sanofi, Genom Med Unit, Framingham, MA USACornell, Cathleen S.论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Genom Med Unit, Framingham, MA USA Sanofi, Genom Med Unit, Framingham, MA USANass, Shelley论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Genom Med Unit, Framingham, MA USA Sanofi, Genom Med Unit, Framingham, MA USAO'Riordan, Catherine论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Genom Med Unit, Framingham, MA USA Sanofi, Genom Med Unit, Framingham, MA USABangari, Dinesh论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Global Discovery Pathol, Framingham, MA USA Sanofi, Genom Med Unit, Framingham, MA USAMueller, Christian论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Genom Med Unit, Framingham, MA USA Sanofi, Genom Med Unit, Framingham, MA USAKyostio-Moore, Sirkka论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Genom Med Unit, Framingham, MA USA Sanofi, Genom Med Unit, Framingham, MA USA
- [24] Adeno-associated virus type 6 is retrogradely transported in the non-human primate brainGENE THERAPY, 2013, 20 (12) : 1178 - 1183San Sebastian, W.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USA Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USASamaranch, L.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USA Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USAHeller, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USA Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USAKells, A. P.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USA Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USABringas, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USA Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USAPivirotto, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USA Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USAForsayeth, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USA Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USABankiewicz, K. S.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USA Univ Calif San Francisco, Dept Neurol Surg, San Francisco, CA 94103 USA
- [25] Use of adeno-associated virus-mediated delivery of mutant huntingtin to study the spreading capacity of the protein in mice and non-human primatesNEUROBIOLOGY OF DISEASE, 2020, 141Maxan, Alexander论文数: 0 引用数: 0 h-index: 0机构: Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, Canada Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, CanadaSciacca, Giacomo论文数: 0 引用数: 0 h-index: 0机构: Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, Canada Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, CanadaAlpaugh, Melanie论文数: 0 引用数: 0 h-index: 0机构: Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, Canada Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, CanadaTao, Zhu论文数: 0 引用数: 0 h-index: 0机构: China Acad Med Sci, Inst Lab Anim Sci, Beijing, Peoples R China Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, CanadaBreger, Ludivine论文数: 0 引用数: 0 h-index: 0机构: Univ Bordeaux, Inst Malad Neurodegenerat, UMR 5293, CNRS UMR 5293, Bordeaux, France CNRS, Inst Malad Neurodegenerat, UMR 5293, F-33076 Bordeaux, France Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, CanadaDehay, Benjamin论文数: 0 引用数: 0 h-index: 0机构: Univ Bordeaux, Inst Malad Neurodegenerat, UMR 5293, CNRS UMR 5293, Bordeaux, France CNRS, Inst Malad Neurodegenerat, UMR 5293, F-33076 Bordeaux, France Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, CanadaLing, Zhang论文数: 0 引用数: 0 h-index: 0机构: China Acad Med Sci, Inst Lab Anim Sci, Beijing, Peoples R China Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, CanadaQin, Chuan论文数: 0 引用数: 0 h-index: 0机构: China Acad Med Sci, Inst Lab Anim Sci, Beijing, Peoples R China Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, Canada论文数: 引用数: h-index:机构:Masnata, Maria论文数: 0 引用数: 0 h-index: 0机构: Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, Canada Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, CanadaSalem, Shireen论文数: 0 引用数: 0 h-index: 0机构: Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, Canada Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, CanadaLacroix, Steve论文数: 0 引用数: 0 h-index: 0机构: Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, Canada Univ Laval, Dept Med Mol, Quebec City, PQ G1K 0A6, Canada Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, CanadaOueslati, Abid论文数: 0 引用数: 0 h-index: 0机构: Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, Canada Univ Laval, Dept Med Mol, Quebec City, PQ G1K 0A6, Canada Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, Canada论文数: 引用数: h-index:机构:Cicchetti, Francesca论文数: 0 引用数: 0 h-index: 0机构: Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, Canada Univ Laval, Dept Psychiat & Neurosci, Quebec City, PQ G1K 0A6, Canada Univ Laval, Axe Neurosci, Ctr Rech, CHU Quebec, Quebec City, PQ G1V 4G2, Canada
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- [27] Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapyPROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 2002, 99 (18) : 11854 - 11859Gao, GP论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Inst Human Gene Therapy, Philadelphia, PA 19104 USAAlvira, MR论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Inst Human Gene Therapy, Philadelphia, PA 19104 USAWang, LL论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Inst Human Gene Therapy, Philadelphia, PA 19104 USACalcedo, R论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Inst Human Gene Therapy, Philadelphia, PA 19104 USAJohnston, J论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Inst Human Gene Therapy, Philadelphia, PA 19104 USAWilson, JM论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Inst Human Gene Therapy, Philadelphia, PA 19104 USA Univ Penn, Inst Human Gene Therapy, Philadelphia, PA 19104 USA
- [28] Physiologically Based Pharmacokinetic Modeling for the Biodistribution of Adeno-Associated Virus Serotype 8 after Intravenous Administration in Mice and Non-Human PrimatesMOLECULAR THERAPY, 2021, 29 (04) : 129 - 130Sun, Kefeng论文数: 0 引用数: 0 h-index: 0机构: Shire Human Genet Therapies, Cambridge, MA USA Shire Human Genet Therapies, Cambridge, MA USAZhang, Zhiwei论文数: 0 引用数: 0 h-index: 0机构: RES Grp Inc, Needham, MA USA Shire Human Genet Therapies, Cambridge, MA USAKo, Glen论文数: 0 引用数: 0 h-index: 0机构: RES Grp Inc, Needham, MA USA Shire Human Genet Therapies, Cambridge, MA USABradshaw, Erica L.论文数: 0 引用数: 0 h-index: 0机构: Takeda Calif Inc, Quantitat Solut, San Diego, CA USA Shire Human Genet Therapies, Cambridge, MA USA
- [29] Second Generation Adeno-Associated Viral Vector Using a Novel Factor VIII Variant with Improved Secretion Achieves Higher Factor VIII Expression in Non-Human PrimatesBLOOD, 2022, 140 : 1902 - 1903Nguyen, Giang N.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USASeleme, Maria C.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USALindgren, Jonathan R.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USAHenriksen, Allysen C.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USAMuehlmatt, Amy论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Comparat Med Serv Core, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USAMcFadden, Melanie论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Comparat Med Serv Core, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USASmith, Geary R.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Comparat Med Serv Core, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USASabatino, Denise E.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Div Hematol, Philadelphia, PA USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA
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Noah论文数: 0 引用数: 0 h-index: 0机构: Seattle Childrens Res Inst, Ctr Global Infect Dis Res, Seattle, WA USA Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USAMontefiori, David论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Dept Surg, Durham, NC 27710 USA Duke Univ, Duke Human Vaccine Inst, Med Ctr, Durham, NC USA Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USASilvestri, Guido论文数: 0 引用数: 0 h-index: 0机构: Scripps Res Inst, Consortium HIV AIDS Vaccine Dev, La Jolla, CA 92037 USA Emory Univ, Yerkes Natl Primate Res Ctr, Atlanta, GA 30322 USA Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USABurton, Dennis R.论文数: 0 引用数: 0 h-index: 0机构: Scripps Res Inst, IAVI Neutralizing Antibody Ctr, La Jolla, CA 92037 USA Scripps Res Inst, Consortium HIV AIDS Vaccine Dev, La Jolla, CA 92037 USA Scripps Res Inst, Dept Immunol & Microbiol, La Jolla, CA USA MIT, Massachusetts Gen Hosp, Ragon Inst, 77 Massachusetts Ave, Cambridge, MA 02139 USA Harvard Univ, Cambridge, MA 02138 USA Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USAMoore, John P.论文数: 0 引用数: 0 h-index: 0机构: Cornell Univ, Weill Med Coll, Dept Microbiol & Immunol, New York, NY 10021 USA Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USAWilson, Ian A.论文数: 0 引用数: 0 h-index: 0机构: Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USA Scripps Res Inst, IAVI Neutralizing Antibody Ctr, La Jolla, CA 92037 USA Scripps Res Inst, Consortium HIV AIDS Vaccine Dev, La Jolla, CA 92037 USA Scripps Res Inst, Skaggs Inst Chem Biol, La Jolla, CA USA Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USASanders, Rogier W.论文数: 0 引用数: 0 h-index: 0机构: Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USA Cornell Univ, Weill Med Coll, Dept Microbiol & Immunol, New York, NY 10021 USA Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USAWard, Andrew B.论文数: 0 引用数: 0 h-index: 0机构: Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USA Scripps Res Inst, IAVI Neutralizing Antibody Ctr, La Jolla, CA 92037 USA Scripps Res Inst, Consortium HIV AIDS Vaccine Dev, La Jolla, CA 92037 USA Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USAvan Gils, Marit J.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Dept Med Microbiol, Amsterdam UMC, Amsterdam, Netherlands Scripps Res Inst, Dept Integrat Struct & Computat Biol, La Jolla, CA 92037 USA