Safety analysis of home-based enzyme replacement therapy with alglucosidase alfa in Pompe disease; a prospective study

被引：0
|
作者：
Ditters, I. [1 ]
van der Ploeg, A. [1 ]
van der Beek, N. [1 ]
van den Hout, J. [1 ]
Huidekoper, H. [1 ]
机构：
[1] Erasmus MC, Rotterdam, Netherlands
来源：
NEUROMUSCULAR DISORDERS | 2022年 / 32卷
关键词：
D O I：
10.1016/j.nmd.2022.07.146
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
VP.29
引用
收藏
页码：S77 / S77
页数：1
相关论文
共 50 条
  • [21] Glycogen storage disease type 2 - Pompe disease - New pathophysiological aspects and current state of enzyme replacement therapy with alglucosidase alfa
    Schoser, B. G. H.
    AKTUELLE NEUROLOGIE, 2007, 34 (05) : 283 - 290
  • [22] A phase 4 prospective study in patients with adult Pompe disease treated with alglucosidase alfa
    Thurberg, Beth L.
    Carlier, Pierre
    Kissel, John T.
    Schoser, Benedikt
    Pestronk, Alan
    Barohn, Richard
    Goker-Alpan, Ozlem
    Mozaffar, Tahseen
    Pena, Loren D. M.
    Simmons, Zachary
    Straub, Volker
    Young, Peter
    Shafi, Raheel
    Bjartmar, Carl
    van der Ploeg, Ans
    MOLECULAR GENETICS AND METABOLISM, 2015, 114 (02) : S113 - S114
  • [23] Safety of home-based infusion of alglucosidase alfa in late onset Pompe disease: 13 years of experience from the Erasmus MC University Medical Center
    Ditters, Imke A. M.
    Van Kooten, Harmke
    van der Beek, Nadine A. M. E.
    van den Hout, Hannerieke
    Huidekoper, Hidde H.
    van der Ploeg, Ans T.
    MOLECULAR GENETICS AND METABOLISM, 2022, 135 (02) : S39 - S39
  • [24] Enzyme replacement therapy with alglucosidase alpha and pregnancy in late-onset Pompe disease
    Santos, M.
    Conceicao, I.
    EUROPEAN JOURNAL OF NEUROLOGY, 2016, 23 : 688 - 688
  • [25] Cessation and resuming of alglucosidase alfa in Pompe disease: a retrospective analysis
    Thomas Hundsberger
    Kai M. Rösler
    Oliver Findling
    Journal of Neurology, 2014, 261 : 1684 - 1690
  • [26] Cessation and resuming of alglucosidase alfa in Pompe disease: a retrospective analysis
    Hundsberger, Thomas
    Roesler, Kai M.
    Findling, Oliver
    JOURNAL OF NEUROLOGY, 2014, 261 (09) : 1684 - 1690
  • [27] Safety of home-based infusion of alglucosidase alfa in late-onset Pompe disease: 13 years of experience from the Erasmus MC university medical center
    Ditters, I.
    van Kooten, H.
    van der Beek, N.
    van den Hout, J.
    Huidekoper, H.
    van der Ploeg, A.
    NEUROMUSCULAR DISORDERS, 2021, 31 : S111 - S111
  • [28] STIG study: real-world data of long-term outcomes of adults with Pompe disease under enzyme replacement therapy with alglucosidase alfa
    Kristina Gutschmidt
    Olimpia Musumeci
    Jordi Díaz-Manera
    Yin-Hsiu Chien
    Karl Christian Knop
    Stephan Wenninger
    Federica Montagnese
    Alessia Pugliese
    Graziana Tavilla
    Jorge Alonso-Pérez
    Paul Wuh-Liang Hwu
    Antonio Toscano
    Benedikt Schoser
    Journal of Neurology, 2021, 268 : 2482 - 2492
  • [29] Pregnancy during enzyme replacement therapy with alglucosidase alfa over a 14-year period in late-onset Pompe disease
    Yanagihara, Chie
    Hayasaka, Yuki
    Kageyama, Yasufumi
    NEUROLOGY AND CLINICAL NEUROSCIENCE, 2023, 11 (02): : 97 - 99
  • [30] STIG study: real-world data of long-term outcomes of adults with Pompe disease under enzyme replacement therapy with alglucosidase alfa
    Gutschmidt, Kristina
    Musumeci, Olimpia
    Diaz-Manera, Jordi
    Chien, Yin-Hsiu
    Knop, Karl Christian
    Wenninger, Stephan
    Montagnese, Federica
    Pugliese, Alessia
    Tavilla, Graziana
    Alonso-Perez, Jorge
    Hwu, Paul Wuh-Liang
    Toscano, Antonio
    Schoser, Benedikt
    JOURNAL OF NEUROLOGY, 2021, 268 (07) : 2482 - 2492
12345