GENETIC THERAPIES Correcting genetic defects with CRISPR-Cas9

被引:9
|
作者
Lokody, Isabel
机构
关键词
D O I
10.1038/nrg3656
中图分类号
Q3 [遗传学];
学科分类号
071007 ; 090102 ;
摘要
引用
收藏
页码:63 / 63
页数:1
相关论文
共 50 条
  • [31] CRISPR-CAS9, BIOSAFETY AND BIOETHICS: A JUSPHILOSOPHICAL AND ENVIRONMENTAL ANALYSIS OF GENETIC ENGINEERING
    Boas Reis, Emilien Vilas
    de Oliveira, Bruno Torquato
    [J]. VEREDAS DO DIREITO, 2019, 16 (34): : 123 - 152
  • [32] Combinatorial CRISPR-Cas9 screens for de novo mapping of genetic interactions
    Shen, John Paul
    Zhao, Dongxin
    Sasik, Roman
    Luebeck, Jens
    Birmingham, Amanda
    Bojorquez-Gomez, Ana
    Licon, Katherine
    Klepper, Kristin
    Pekin, Daniel
    Beckett, Alex N.
    Sanchez, Kyle Salinas
    Thomas, Alex
    Kuo, Chih-Chung
    Du, Dan
    Roguev, Assen
    Lewis, Nathan E.
    Chang, Aaron N.
    Kreisberg, Jason F.
    Krogan, Nevan
    Qi, Lei
    Ideker, Trey
    Mali, Prashant
    [J]. NATURE METHODS, 2017, 14 (06) : 573 - +
  • [33] CRISPR-Cas9 therapies in experimental mouse models of cancer
    Estevao, Diogo
    Costa, Natalia Rios
    da Costa, Rui Gil
    Medeiros, Rui
    [J]. FUTURE ONCOLOGY, 2018, 14 (20) : 2082 - 2094
  • [34] CRISPR-Cas9 Gene Editing: Curing Genetic Diseases by Inherited Epigenetic Modifications
    Kolanu, Nikhil Deep
    [J]. GLOBAL MEDICAL GENETICS, 2024, 11 (01): : 113 - 122
  • [35] Modelling genetic heterogeneity as a resistance mechanism to cancer immunotherapy using CRISPR-Cas9
    Glodde, N.
    Bald, T.
    van den Boorn-Konijnenberg, D.
    Schmid-Burgk, J.
    Hornung, V.
    Tueting, T.
    Hoelzel, M.
    [J]. EXPERIMENTAL DERMATOLOGY, 2016, 25 (03) : E42 - E42
  • [36] Functional genetic screens for enhancer elements in the human genome using CRISPR-Cas9
    Korkmaz, Gozde
    Lopes, Rui
    Ugalde, Alejandro P.
    Nevedomskaya, Ekaterina
    Han, Ruiqi
    Myacheva, Ksenia
    Zwart, Wilbert
    Elkon, Ran
    Agami, Reuven
    [J]. NATURE BIOTECHNOLOGY, 2016, 34 (02) : 192 - +
  • [37] Functional genetic screens for enhancer elements in the human genome using CRISPR-Cas9
    Gozde Korkmaz
    Rui Lopes
    Alejandro P Ugalde
    Ekaterina Nevedomskaya
    Ruiqi Han
    Ksenia Myacheva
    Wilbert Zwart
    Ran Elkon
    Reuven Agami
    [J]. Nature Biotechnology, 2016, 34 : 192 - 198
  • [38] Development of a plasmid free CRISPR-Cas9 system for the genetic modification of Mucor circinelloides
    Nagy, Gabor
    Szebenyi, Csilla
    Csernetics, Arpad
    Vaz, Amanda Grace
    Toth, Eszter Judit
    Vagvolgyi, Csaba
    Papp, Tamas
    [J]. SCIENTIFIC REPORTS, 2017, 7
  • [39] Revitalizing oral cancer research: Crispr-Cas9 technology the promise of genetic editing
    Sowmya, S. V.
    Augustine, Dominic
    Mushtaq, Shazia
    Baeshen, Hosam Ali
    Ashi, Heba
    Hassan, Reem Nabil
    Alshahrani, Mohammed
    Patil, Shankargouda
    [J]. FRONTIERS IN ONCOLOGY, 2024, 14
  • [40] Development of a plasmid free CRISPR-Cas9 system for the genetic modification of Mucor circinelloides
    Gábor Nagy
    Csilla Szebenyi
    Árpád Csernetics
    Amanda Grace Vaz
    Eszter Judit Tóth
    Csaba Vágvölgyi
    Tamás Papp
    [J]. Scientific Reports, 7