CFTR MODULATOR THERAPY FOR CYSTIC FIBROSIS CAUSED BY THE RARE C.3700A>G MUTATION

被引:0
|
作者
Phuan, P. [1 ]
Haggie, P. M. [1 ]
Tan, J. T. [1 ]
Rivera, A. [1 ]
Finkbeiner, W. [1 ]
Nielson, D. W. [1 ]
Thomas, M. [2 ]
Janahi, I. A. [3 ]
Verkman, A. S. [1 ]
机构
[1] UC San Francisco, Dept Med, San Francisco, CA USA
[2] Hamad Med Corp, Dept Chest, Doha, Ad Dawhah, Qatar
[3] Sidra Med & Res Ctr, Pediat Med, Doha, Ad Dawhah, Qatar
关键词
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中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
440
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页码:S210 / S210
页数:1
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