共 50 条
- [21] Combined therapy of imiglucerase and miglustat in Gaucher disease with severe bone complicationsPRESSE MEDICALE, 2009, 38 : 2S68 - 2S70Marie, Isabelle论文数: 0 引用数: 0 h-index: 0机构: CHU Rouen Bois Guillaume, Dept Med Interne, F-76031 Rouen, France CHU Rouen Bois Guillaume, Dept Med Interne, F-76031 Rouen, France
- [22] Short-term effect of oral treatment with miglustat in type 1 Gaucher disease.BLOOD, 2005, 106 (11) : 629A - 630AGiraldo, P论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, SpainAlonso, D论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, SpainAcedo, M论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, SpainFranco, R论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, SpainBarez, A论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, SpainCorrales, A论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, SpainSerrano, D论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, SpainRoldan, V论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, SpainLatre, P论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, SpainAlfonso, P论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, SpainPocovi, M论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, Spain
- [23] Twelve years of experience with miglustat in the treatment of type 1 Gaucher disease: The Spanish ZAGAL projectBLOOD CELLS MOLECULES AND DISEASES, 2018, 68 : 173 - 179Giraldo, Pilar论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Haematol, Zaragoza, Spain CIBER Enfermedades Raras CIBERER, Valencia, Spain Spanish Fdn Study & Therapy Gaucher Dis FEETEG, Zaragoza, Spain Inst Hlth Res Aragon IIS Aragon, Zaragoza, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainAndrade-Campos, Marcio论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Haematol, Zaragoza, Spain CIBER Enfermedades Raras CIBERER, Valencia, Spain Spanish Fdn Study & Therapy Gaucher Dis FEETEG, Zaragoza, Spain Inst Hlth Res Aragon IIS Aragon, Zaragoza, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainAlfonso, Pilar论文数: 0 引用数: 0 h-index: 0机构: CIBER Enfermedades Raras CIBERER, Valencia, Spain Spanish Fdn Study & Therapy Gaucher Dis FEETEG, Zaragoza, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainIrun, Pilar论文数: 0 引用数: 0 h-index: 0机构: CIBER Enfermedades Raras CIBERER, Valencia, Spain Zaragoza Univ, Biochem & Mol & Cellular Biol, Zaragoza, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainAtutxa, Koldo论文数: 0 引用数: 0 h-index: 0机构: Galdakao Hosp, Haematol, Usansolo, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainAcedo, Antonio论文数: 0 引用数: 0 h-index: 0机构: Vega Baja Hosp, Haematol, Alicante, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainBarez, Abelardo论文数: 0 引用数: 0 h-index: 0机构: Ntra Sra Sonsoles Hosp, Haematol, Avila, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainBlanes, Margarita论文数: 0 引用数: 0 h-index: 0机构: Virgen Salud Hosp, Haematol, Elda, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainDiaz-Morant, Vicente论文数: 0 引用数: 0 h-index: 0机构: Ronda Hosp, Internal Med, Ronda, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainAngeles Fernandez-Galan, Ma论文数: 0 引用数: 0 h-index: 0机构: Virgen Puerto Hosp, Plasencia, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainFranco, Rafael论文数: 0 引用数: 0 h-index: 0机构: Punta Europa Univ Hosp, Haematol, Cadiz, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainGil-Cortes, Cristina论文数: 0 引用数: 0 h-index: 0机构: San Vicente Hosp, Haematol, Alicante, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainGiner, Vicente论文数: 0 引用数: 0 h-index: 0机构: Virgen Lirios Hosp, Internal Med, Alcoy, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainIbanez, Angela论文数: 0 引用数: 0 h-index: 0机构: Complejo Hosp Albacete, Haematol, Albacete, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainLatre, Paz论文数: 0 引用数: 0 h-index: 0机构: Spanish Fdn Study & Therapy Gaucher Dis FEETEG, Zaragoza, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainLoyola, Ines论文数: 0 引用数: 0 h-index: 0机构: Complexo Hosp Pontevedra, Haematol, Pontevedra, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainLuno, Elisa论文数: 0 引用数: 0 h-index: 0机构: Cent Asturias Univ Hosp, Haematol, Oviedo, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainHernandez-Martin, Roberto论文数: 0 引用数: 0 h-index: 0机构: Virgen Concha Hosp, Haematol, Zamora, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainMedrano-Engay, Blanca论文数: 0 引用数: 0 h-index: 0机构: Inst Hlth Res Aragon IIS Aragon, Zaragoza, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainPuerta, Jose论文数: 0 引用数: 0 h-index: 0机构: Virgen Nieves Hosp Granada, Haematol, Granada, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainRoig, Inmaculada论文数: 0 引用数: 0 h-index: 0机构: Parc Tauli Hosp, Haematol, Sabadell, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, Spainde la Serna, Javier论文数: 0 引用数: 0 h-index: 0机构: Doce Octubre Univ Hosp, Haematol, Madrid, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainSalamero, Olga论文数: 0 引用数: 0 h-index: 0机构: Vall dHebron Univ Hosp, Haematol, Barcelona, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainVillalon, Lucia论文数: 0 引用数: 0 h-index: 0机构: Alcorcon Hosp, Haematol, Madrid, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, SpainPocovi, Miguel论文数: 0 引用数: 0 h-index: 0机构: Inst Hlth Res Aragon IIS Aragon, Zaragoza, Spain Zaragoza Univ, Biochem & Mol & Cellular Biol, Zaragoza, Spain Miguel Servet Univ Hosp, Haematol, Zaragoza, Spain
- [24] Two-year oral miglustat in Gaucher disease type IIIMOLECULAR GENETICS AND METABOLISM, 2007, 92 (04) : S33 - S33Schiffmann, Raphael论文数: 0 引用数: 0 h-index: 0机构: NIH, NINDS, Bethesda, MD 20892 USA NIH, NINDS, Bethesda, MD 20892 USAChris, Harris论文数: 0 引用数: 0 h-index: 0机构: Univ Plymouth, Plymouth PL4 8AA, Devon, England NIH, NINDS, Bethesda, MD 20892 USACatherine, DeVile论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London WC1E 6BT, England NIH, NINDS, Bethesda, MD 20892 USAElin, Davis-Pope论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, Melbourne, Vic, Australia NIH, NINDS, Bethesda, MD 20892 USAEd, Fitzgibbon论文数: 0 引用数: 0 h-index: 0机构: NIH, Bethesda, MD 20892 USA NIH, NINDS, Bethesda, MD 20892 USARoscoe, Brady论文数: 0 引用数: 0 h-index: 0机构: NIH, Bethesda, MD 20892 USA NIH, NINDS, Bethesda, MD 20892 USA论文数: 引用数: h-index:机构:Pauline, Campbell论文数: 0 引用数: 0 h-index: 0机构: Univ Plymouth, Plymouth PL4 8AA, Devon, England NIH, NINDS, Bethesda, MD 20892 USAAshok, Vellodi论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London WC1E 6BT, England NIH, NINDS, Bethesda, MD 20892 USA
- [25] TEN YEARS OF EXPERIENCE WITH MIGLUSTAT IN TREATMENT OF TYPE 1 GAUCHER DISEASE: THE SPANISH ZAGAL PROJECTHAEMATOLOGICA, 2014, 99 : 764 - 764Giraldo, P.论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, Spain Miguel Servet Univ Hosp, Traslat Res Unit, Zaragoza, Spain ISCIII, CIBERER, Madrid, Spain Miguel Servet Univ Hosp, Zaragoza, SpainAndrade, M.论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, Spain Miguel Servet Univ Hosp, Traslat Res Unit, Zaragoza, Spain Miguel Servet Univ Hosp, Zaragoza, SpainAlfonso, P.论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Traslat Res Unit, Zaragoza, Spain ISCIII, CIBERER, Madrid, Spain Miguel Servet Univ Hosp, Zaragoza, SpainIrun, P.论文数: 0 引用数: 0 h-index: 0机构: ISCIII, CIBERER, Madrid, Spain Miguel Servet Univ Hosp, Zaragoza, SpainAtucha, L.论文数: 0 引用数: 0 h-index: 0机构: Hosp Basurto, Bilbao, Spain Miguel Servet Univ Hosp, Zaragoza, SpainAcedo, A.论文数: 0 引用数: 0 h-index: 0机构: Gen Hosp, Valencia, Spain Miguel Servet Univ Hosp, Zaragoza, SpainDiaz-Morant, V.论文数: 0 引用数: 0 h-index: 0机构: Hosp Malaga, Malaga, Spain Miguel Servet Univ Hosp, Zaragoza, SpainBarez, A.论文数: 0 引用数: 0 h-index: 0机构: Hosp Ntr Sra de Sonsoles, Avila, Spain Miguel Servet Univ Hosp, Zaragoza, SpainFernandez-Galan, M.论文数: 0 引用数: 0 h-index: 0机构: Hosp Virgen del Puerto, Plasencia, Spain Miguel Servet Univ Hosp, Zaragoza, SpainFranco, R.论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, Spain Miguel Servet Univ Hosp, Traslat Res Unit, Zaragoza, Spain Miguel Servet Univ Hosp, Zaragoza, SpainGiner, V.论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, Spain ISCIII, CIBERER, Madrid, Spain Miguel Servet Univ Hosp, Zaragoza, SpainLoyola, I.论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, Spain Miguel Servet Univ Hosp, Zaragoza, SpainLuno, E.论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, Spain Miguel Servet Univ Hosp, Zaragoza, Spainde la Serna, J.论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, Spain Univ Zaragoza, Zaragoza, Spain Miguel Servet Univ Hosp, Zaragoza, SpainVillalon, L.论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, Spain Hosp Basurto, Bilbao, Spain Miguel Servet Univ Hosp, Zaragoza, SpainSalamero, O.论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, Spain Gen Hosp, Valencia, Spain Miguel Servet Univ Hosp, Zaragoza, SpainPocovi, M.论文数: 0 引用数: 0 h-index: 0机构: Miguel Servet Univ Hosp, Zaragoza, Spain
- [26] Randomized, Controlled Trial of Miglustat in Gaucher's Disease Type 3ANNALS OF NEUROLOGY, 2008, 64 (05) : 514 - 522Schiffmann, Raphael论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USA Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USAFitzgibbon, Edmond J.论文数: 0 引用数: 0 h-index: 0机构: NEI, NIH, Bethesda, MD 20892 USA Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USAHarris, Chris论文数: 0 引用数: 0 h-index: 0机构: Univ Plymouth, Ctr Theoret & Computat Neurosci, Plymouth PL4 8AA, Devon, England Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USADeVile, Catherine论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, London WC1N 3JH, England Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USADavies, Elin H.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, London WC1N 3JH, England Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USAAbel, Larry论文数: 0 引用数: 0 h-index: 0机构: Univ Melbourne, Dept Optometry & Vis Sci, Melbourne, Vic, Australia Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USAvan Schaik, Ivo N.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Neurol & Clin Neurophysiol, NL-1105 AZ Amsterdam, Netherlands Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USABenko, William论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USA Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USATimmons, Margaret论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USA Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USARies, Markus论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USA Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USAVellodi, Ashok论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, London WC1N 3JH, England Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branch, Bethesda, MD USA
- [27] Miglustat Therapy in Type 1 Gaucher Disease: Long-Term Treatment Experience From a Multicenter, Retrospective Cohort StudyBLOOD, 2011, 118 (21) : 1385 - 1385Kuter, David J.论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Massachusetts Gen Hosp, Sch Med, Boston, MA USA Harvard Univ, Massachusetts Gen Hosp, Sch Med, Boston, MA USAMehta, Atul论文数: 0 引用数: 0 h-index: 0机构: Royal Free Hosp, London NW3 2QG, England UCL, Sch Med, London W1N 8AA, England Harvard Univ, Massachusetts Gen Hosp, Sch Med, Boston, MA USA论文数: 引用数: h-index:机构:Giraldo, Pilar论文数: 0 引用数: 0 h-index: 0机构: Minist Publ Hlth Russia, Hematol Res Ctr, Moscow, Russia Harvard Univ, Massachusetts Gen Hosp, Sch Med, Boston, MA USAHughes, Derralynn论文数: 0 引用数: 0 h-index: 0机构: Royal Free Hosp, London NW3 2QG, England UCL, Sch Med, London W1N 8AA, England Harvard Univ, Massachusetts Gen Hosp, Sch Med, Boston, MA USABelmatoug, Nadia论文数: 0 引用数: 0 h-index: 0机构: Hop Beaujon, Clichy, France Harvard Univ, Massachusetts Gen Hosp, Sch Med, Boston, MA USABrand, Monika论文数: 0 引用数: 0 h-index: 0机构: Actel Pharmaceut, Allschwil, Switzerland Harvard Univ, Massachusetts Gen Hosp, Sch Med, Boston, MA USAMuller, Audrey论文数: 0 引用数: 0 h-index: 0机构: Actel Pharmaceut, Allschwil, Switzerland Harvard Univ, Massachusetts Gen Hosp, Sch Med, Boston, MA USASchaaf, Berthold论文数: 0 引用数: 0 h-index: 0机构: Factum, Offenbach, Germany Harvard Univ, Massachusetts Gen Hosp, Sch Med, Boston, MA USAGiorgino, Ruben论文数: 0 引用数: 0 h-index: 0机构: Actel Pharmaceut, Allschwil, Switzerland Harvard Univ, Massachusetts Gen Hosp, Sch Med, Boston, MA USAZimran, Ari论文数: 0 引用数: 0 h-index: 0机构: Shaare Zedek Med Ctr, Jerusalem, Israel Harvard Univ, Massachusetts Gen Hosp, Sch Med, Boston, MA USA
- [28] Enzyme replacement therapy in romanian patients with type 1 Gaucher diseaseCLINICAL THERAPEUTICS, 2007, 29 : S118 - S118Sido, P. Grigorescu论文数: 0 引用数: 0 h-index: 0机构: Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, Romania Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, RomaniaDrugan, C.论文数: 0 引用数: 0 h-index: 0机构: Iuliu Hatieganu Univ Med & Pharm, Dept Biochem, Cluj Napoca, Romania Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, RomaniaCret, V.论文数: 0 引用数: 0 h-index: 0机构: Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, Romania Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, RomaniaAl-Kzouz, C.论文数: 0 引用数: 0 h-index: 0机构: Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, Romania Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, RomaniaDenes, C.论文数: 0 引用数: 0 h-index: 0机构: Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, Romania Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, RomaniaZimmermann, A.论文数: 0 引用数: 0 h-index: 0机构: Johannes Gutenberg Univ Mainz, Dept Endocrinol & Diabetol, Clin Internal Med 1, Mainz, Germany Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, RomaniaColdea, C.论文数: 0 引用数: 0 h-index: 0机构: Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, Romania Iuliu Hatieganu Univ Med & Pharm, Pediat Clin 1, Cluj Napoca, Romania
- [29] MIGLUSTAT THERAPY IN TYPE 1 GAUCHER DISEASE: LONG-TERM TREATMENT EXPERIENCE FROM A MULTICENTER, RETROSPECTIVE COHORT STUDYJOURNAL OF INHERITED METABOLIC DISEASE, 2012, 35 : S97 - S97Hollak, C. E. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, NetherlandsKuter, D.论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Boston, MA 02114 USA Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, NetherlandsGiraldo, P.论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Miguel Servet, CIBERER, Zaragoza, Spain Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, NetherlandsHughes, D.论文数: 0 引用数: 0 h-index: 0机构: Royal Free Hosp, London NW3 2QG, England Univ Coll Med Sch, London, England Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, NetherlandsBelmatoug, N.论文数: 0 引用数: 0 h-index: 0机构: Hop Beaujon, Clichy, France Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, NetherlandsBrand, M.论文数: 0 引用数: 0 h-index: 0机构: Actel Pharmaceut Ltd, Allschwil, Switzerland Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, NetherlandsMuller, A.论文数: 0 引用数: 0 h-index: 0机构: Actel Pharmaceut Ltd, Allschwil, Switzerland Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, NetherlandsSchaaf, B.论文数: 0 引用数: 0 h-index: 0机构: Factum, Offenbach, Germany Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, NetherlandsGiorgino, R.论文数: 0 引用数: 0 h-index: 0机构: Actel Pharmaceut Ltd, Allschwil, Switzerland Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, NetherlandsZimran, A.论文数: 0 引用数: 0 h-index: 0机构: Shaare Zedek Med Ctr, Jerusalem, Israel Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, Netherlands
- [30] Substrate Reduction Therapy With Miglustat In Type 1 Gaucher Disease In Spain. Nine Years Outcomes Update On ZAGAL StudyBLOOD, 2013, 122 (21)Giraldo, Pilar论文数: 0 引用数: 0 h-index: 0Andrade, Marcio M., Sr.论文数: 0 引用数: 0 h-index: 0Medrano, Blanca论文数: 0 引用数: 0 h-index: 0Alfonso, Pilar论文数: 0 引用数: 0 h-index: 0Irun, Pilar论文数: 0 引用数: 0 h-index: 0Atutxa, Koldo论文数: 0 引用数: 0 h-index: 0Fernandez-Galan, Angeles论文数: 0 引用数: 0 h-index: 0Barez, Abelardo论文数: 0 引用数: 0 h-index: 0Franco, Rafael论文数: 0 引用数: 0 h-index: 0Roig, Inmaculada论文数: 0 引用数: 0 h-index: 0Giner, Vicente论文数: 0 引用数: 0 h-index: 0Villalon, Lucia论文数: 0 引用数: 0 h-index: 0Martinez-Estefano, Elisa论文数: 0 引用数: 0 h-index: 0Luno, Elisa论文数: 0 引用数: 0 h-index: 0Loyola, Ines论文数: 0 引用数: 0 h-index: 0Salamero, Olga论文数: 0 引用数: 0 h-index: 0de la Serna, Javier论文数: 0 引用数: 0 h-index: 0Pocovi, Miguel论文数: 0 引用数: 0 h-index: 0