The 6 min walk test (6MWT) as a clinical trial outcome measure in Duchenne/Becker Muscular Dystrophy (DMD/BMD)

被引：2
|
作者：
McDonald, C. M. [1 ]
Henricson, E. K. [1 ]
Han, J. J. [1 ]
Nicorici, A. R. [1 ]
Abresch, R. T. [1 ]
Atkinson, L. A. [2 ]
Reha, A. L. [2 ]
Elfring, G. L. [2 ]
Miller, L. L. [2 ]
机构：
[1] Univ Calif Davis, Davis Med Ctr, Sacramento, CA 95817 USA
[2] PTC Therapeut, S Plainfield, NJ USA
来源：
NEUROMUSCULAR DISORDERS | 2008年 / 18卷 / 9-10期
关键词：
D O I：
10.1016/j.nmd.2008.06.054
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：739 / 739
页数：1
相关论文
共 50 条
  • [21] Comparative economic impact of therapeutic innovation on health care burden of Duchenne Muscular Dystrophy (DMD) using Becker Muscular Dystrophy (BMD) as a comparator for potential clinical outcome corridor
    Schreiber, O.
    Klug, C.
    Thiele, S.
    Schorling, E.
    Zowe, J.
    Reilich, P.
    Nagels, K.
    Walter, M. C.
    NEUROMUSCULAR DISORDERS, 2014, 24 (9-10) : 855 - 855
  • [22] Changes in the six minute walk test (6MWT) in Pompe disease
    Dubrovsky, A.
    Chloca, F.
    Corderi, J. R.
    Jauregui, A.
    NEUROMUSCULAR DISORDERS, 2013, 23 (9-10) : 827 - 827
  • [23] Genotypic spectrum of Duchenne and Becker muscular dystrophy (DMD/BMD) in an Indian, South African and Brazilian cohort
    Perry, L.
    Reyaz, A.
    Human, R.
    Lubbe, E.
    Raga, S.
    Naidu, K.
    Tomaselli, P.
    Vandrovcova, J.
    Hanna, M.
    Marques, W., Jr.
    Henning, F.
    Heckmann, J.
    Wilmshurst, J.
    Vishnu, V.
    Srivastava, M.
    Yareeda, S.
    Smuts, I.
    Sarkozy, A.
    Muntoni, F.
    NEUROMUSCULAR DISORDERS, 2023, 33 : S147 - S147
  • [24] The 6-Minute Walk Test in Duchenne Muscular Dystrophy: Longitudinal Observations
    McDonald, Craig
    Henricson, Erik
    Abresch, Richard
    Han, Jay
    Nicorici, Alina
    Goude, Erica
    Elfring, Gary
    Reha, Allen
    Hirawat, Samit
    Miller, Langdon
    NEUROLOGY, 2010, 74 (09) : A219 - A219
  • [25] RELIABILITY AND VALIDITY OF THE 6-MINUTE WALK TEST AS AN OUTCOME MEASURE IN OCULOPHARYNGEAL MUSCULAR DYSTROPHY
    Fernandez, M.
    Youssof, S.
    JOURNAL OF INVESTIGATIVE MEDICINE, 2016, 64 (01) : 344 - 345
  • [26] Movement monitoring at home and during study visits identifies sources of variability in 6MWT performance in Duchenne muscular dystrophy
    Servais, L.
    Grelet, M.
    Seferian, A.
    Gasnier, E.
    Gargaun, E.
    Straub, V.
    Mercuri, E.
    Voit, T.
    Laforet, G.
    Dorveau, E.
    Vissiere, D.
    Muntoni, F.
    NEUROMUSCULAR DISORDERS, 2016, 26 : S152 - S153
  • [27] ASCERTAINMENT AND GENETIC-COUNSELING OF RISK FAMILIES WITH DUCHENNE MUSCULAR-DYSTROPHY (DMD) OR BECKER MUSCULAR-DYSTROPHY (BMD) IN THE DISTRICT ERFURT
    SPIEGLER, AWJ
    HERRMANN, FH
    DEUTSCHE GESUNDHEITSWESEN-ZEITSCHRIFT FUR KLINISCHE MEDIZIN, 1983, 38 (26): : 994 - 1000
  • [28] Pulmonary function and 6-min walk test (6MWT) among North African long COVID-19 patients
    Derbel, K.
    Sellami, S.
    Benzarti, W.
    Aissa, S.
    Rouatbi, S.
    Ben Saad, H.
    Ghannouchi, I.
    EUROPEAN RESPIRATORY JOURNAL, 2022, 60
  • [29] Comprehensive genetic diagnosis of patients with Duchenne/Becker muscular dystrophy (DMD/BMD) and pathogenicity analysis of splice site variants in the DMD gene
    Yang, Yan-mei
    Yan, Kai
    Liu, Bei
    Chen, Min
    Wang, Li-ya
    Huang, Ying-zhi
    Qian, Ye-qing
    Sun, Yi-xi
    Li, Hong-ge
    Dong, Min-yue
    JOURNAL OF ZHEJIANG UNIVERSITY-SCIENCE B, 2019, 20 (09): : 753 - 765
  • [30] RELIABILITY AND VALIDITY OF THE 6-MINUTE WALK TEST AS AN OUTCOME MEASURE IN OCULO-PHARYNGEAL MUSCULAR DYSTROPHY
    Youssof, S.
    Fernandez, M.
    MUSCLE & NERVE, 2015, 52 : S5 - S5
12345