Comparison of CNS Transduction by Different AAV Capsids in Mouse and Non-Human Primate

被引:0
|
作者
Goulet, Martin [1 ]
Aubin, Justin [1 ]
Kells, Adrian P. [1 ]
Su, Qin [2 ]
Yuan, Shipeng [1 ]
Ramamoorthi, Kartik [1 ]
Kotin, Rob [1 ]
McLaughlin, James [1 ]
Gao, Guangping [2 ]
Sah, Dinah W. Y. [1 ]
机构
[1] Voyager Therapeut, Neurosci, Cambridge, MA USA
[2] UMMS, Gene Therapy Ctr, Worcester, MA USA
关键词
D O I
10.1016/S1525-0016(16)33691-7
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
86
引用
收藏
页码:S37 / S37
页数:1
相关论文
共 50 条
  • [41] Intravitreal injection of a rationally designed AAV capsid library in non-human primate identifies variants with enhanced retinal transduction and neutralizing antibody evasion
    Kellish, Patrick C.
    Marsic, Damien
    Crosson, Sean M.
    Choudhury, Shreyasi
    Scalabrino, Miranda L.
    Strang, Christianne E.
    Hill, Julie
    McCullough, K. Tyler
    Peterson, James J.
    Fajardo, Diego
    Gupte, Siddhant
    Makal, Victoria
    Kondratov, Oleksandr
    Kondratova, Liudmyla
    Iyer, Siva
    Witherspoon, C. Douglas
    Gamlin, Paul D.
    Zolotukhin, Sergei
    Boye, Sanford L.
    Boye, Shannon E.
    MOLECULAR THERAPY, 2023, 31 (12) : 3441 - 3456
  • [42] Neuropathogenesis of Encephalitic Alphaviruses in Non-Human Primate and Mouse Models of Infection
    Woodson, Caitlin M.
    Carney, Shannon K.
    Kehn-Hall, Kylene
    PATHOGENS, 2025, 14 (02):
  • [43] The grey mouse lemur: A non-human primate model for ageing studies
    Languille, S.
    Blanc, S.
    Blin, O.
    Canale, C. I.
    Dal-Pan, A.
    Devau, G.
    Dhenain, M.
    Dorieux, O.
    Epelbaum, J.
    Gomez, D.
    Hardy, I.
    Henry, P. -Y.
    Irving, E. A.
    Marchal, J.
    Mestre-Frances, N.
    Perret, M.
    Picq, J-L.
    Pifferi, F.
    Rahman, A.
    Schenker, E.
    Terrien, J.
    Thery, M.
    Verdier, J. -M.
    Aujard, F.
    AGEING RESEARCH REVIEWS, 2012, 11 (01) : 150 - 162
  • [44] Mouse and Non-human Primate Models for EV71 Disease
    Shimizu, H.
    INTERNATIONAL JOURNAL OF INFECTIOUS DISEASES, 2008, 12 : E13 - E13
  • [45] RNA-Driven Evolution of AAV Capsid Libraries Identifies Variants with High Transduction Efficiency in Non-Human Primate Central Nervous System
    Nonnenmacher, Mathieu
    Li, Shaoyong
    Wang, Wei
    Child, Matthew A.
    Ren, Amy Z.
    Tyson, Katherine
    Pande, Nilesh
    Lu, Xiaodong
    Li, Jiangyu
    Ren, Xiao-Qin
    Shang, Jianyu
    Hefferan, Michael
    Hou, Jay
    Khwaja, Omar
    MOLECULAR THERAPY, 2021, 29 (04) : 25 - 26
  • [46] Developing a CRISPR Tool to Facilitate Quantification of AAV Transduction in the Mouse CNS
    Lo, Shih-Ching
    McCampbell, Alex
    MOLECULAR THERAPY, 2019, 27 (04) : 342 - 342
  • [47] Comparable efficiency of photoreceptor transduction by AAV2tYF, AAV5 and AAV8 in non-human primates
    Shearman, M. S.
    Song, C. J.
    Ye, G.
    Timmers, A. M.
    Newmark, J.
    HUMAN GENE THERAPY, 2018, 29 (12) : A153 - A153
  • [48] CNS LEVELS OF PANOBINOSTAT IN A NON-HUMAN PRIMATE MODEL: COMPARISON OF BLOOD AND CEREBROSPINAL FLUID PHARMACOKINETIC METHODS AND MALDI MSI
    Warren, Katherine
    McCully, Cynthia Lester
    Garcia, Rafael Cruz
    Stopka, Sylwia
    Regan, Michael
    Aye, Thet
    Zimmerman, Sara
    Peer, Cody
    Kramer, Josh
    Breed, Matthew
    Figg, W. Douglas
    Agar, Nathalie
    NEURO-ONCOLOGY, 2021, 23 : 48 - 48
  • [49] In vivo selection in non-human primates identifies AAV capsids for on-target CSF delivery to spinal cord
    Hanlon, Killian S.
    Cheng, Ming
    Ferrer, Roberto Montoro
    Ryu, Jae Ryun
    Lee, Boram
    de la Cruz, Demitri
    Patel, Nikita
    Espinoza, Paula
    Santoscoy, Miguel C.
    Gong, Yi
    Ng, Carrie
    Nguyen, Diane M.
    Nammour, Josette
    Clark, Sean W.
    Heine, Vivi M.
    Sun, Woong
    Kozarsky, Karen
    Maguire, Casey A.
    MOLECULAR THERAPY, 2024, 32 (08) : 2584 - 2603
  • [50] Neutralizing anti-AAV antibody impact on vector transduction following intravitreal administration of AAV in non-human primates
    Shearman, M. S.
    Turunen, H. T.
    Newmark, J.
    Pennock, S.
    Timmers, A.
    HUMAN GENE THERAPY, 2019, 30 (11) : A115 - A116