Nanoemulsions as non-viral vectors of the CRISPR/Cas9 system aiming for MPS I gene editing

被引:0
|
作者
Schuh, R. S. [1 ]
Carvalho, T. G. [1 ]
Bidone, J. [1 ]
Pasqualim, G. [1 ]
Diel, D. [1 ]
Teixeira, H. F. [1 ]
Baldo, G. [1 ]
机构
[1] Univ Fed Rio Grande do Sul, Porto Alegre, RS, Brazil
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
P291
引用
收藏
页码:A134 / A134
页数:1
相关论文
共 50 条
  • [41] Development of a CRISPR/Cas9 System for Methylococcus capsulatus In Vivo Gene Editing
    Tapscott, Timothy
    Guarnieri, Michael T.
    Henard, Calvin A.
    APPLIED AND ENVIRONMENTAL MICROBIOLOGY, 2019, 85 (11)
  • [42] Efficient gene editing in Corynebacterium glutamicum using the CRISPR/Cas9 system
    Peng, Feng
    Wang, Xinyue
    Sun, Yang
    Dong, Guibin
    Yang, Yankun
    Liu, Xiuxia
    Bai, Zhonghu
    MICROBIAL CELL FACTORIES, 2017, 16
  • [43] Brain and visceral gene editing of mucopolysaccharidosis I mice by nasal delivery of the CRISPR/Cas9 system
    Pimentel Vera, Luisa Natalia
    Schuh, Roselena Silvestri
    Silveira Fachel, Flavia Nathielly
    Poletto, Edina
    Piovesan, Eduarda
    Kubaski, Francyne
    Couto, Eduarda
    Brum, Bruna
    Rodrigues, Graziella
    Souza, Hallana
    Giugliani, Roberto
    Matte, Ursula
    Baldo, Guilherme
    Teixeira, Helder F.
    JOURNAL OF GENE MEDICINE, 2022, 24 (04):
  • [44] CRISPR/CAS9 GENE EDITING TO BLOCK MALARIA TRANSMISSION
    Simoes, Maria
    Dong, Yuemei
    Dimopoulos, George
    AMERICAN JOURNAL OF TROPICAL MEDICINE AND HYGIENE, 2018, 99 (04): : 262 - 262
  • [45] CRISPR/Cas9 gene editing therapies for cystic fibrosis
    Graham, Carina
    Hart, Stephen
    EXPERT OPINION ON BIOLOGICAL THERAPY, 2021, 21 (06) : 767 - 780
  • [46] CRISPR/Cas9 gene editing for genodermatoses: progress and perspectives
    Naso, Gaetano
    Petrova, Anastasia
    EMERGING TOPICS IN LIFE SCIENCES, 2019, 3 (03) : 313 - 326
  • [47] The enhancement of CRISPR/Cas9 gene editing using metformin
    Rollins, Jaedyn L.
    Hall, Raquel M.
    Lemus, Clara J.
    Leisten, Lauren A.
    Johnston, Jennifer M.
    BIOCHEMISTRY AND BIOPHYSICS REPORTS, 2023, 35
  • [48] CRISPR/CAS9 GENE EDITING APPLICATIONS IN CARDIOVASCULAR DISEASE
    Khouzam, J.
    Khouzam, R.
    Tivakaran, V.
    JOURNAL OF INVESTIGATIVE MEDICINE, 2021, 69 (02) : 423 - 424
  • [49] Delivery methods for CRISPR/Cas9 gene editing in crustaceans
    Xu, Sen
    Pham, Thinh
    Neupane, Swatantra
    MARINE LIFE SCIENCE & TECHNOLOGY, 2020, 2 (01) : 1 - 5
  • [50] Therapeutic gene editing in haematological disorders with CRISPR/Cas9
    Jensen, Trine I.
    Axelgaard, Esben
    Bak, Rasmus O.
    BRITISH JOURNAL OF HAEMATOLOGY, 2019, 185 (05) : 821 - 835