iPSC-based strategy to correct the bleeding phenotype in haemophilia A

被引:0
|
作者
Talmon, M. [1 ]
Ranaldo, G. [1 ]
Olgasi, C. [1 ]
Lombardo, A. [2 ]
Merlin, S. [1 ]
Cannizzo, E. S. [1 ]
Raya, A. [3 ]
Naldini, L. [2 ]
Schinco, P. [4 ]
Follenzi, A. [1 ]
机构
[1] Univ Piemonte Orientale, Novara, Italy
[2] H San Raffaele, Tiget, Milan, Italy
[3] Inst Bioengn Catalonia, Barcelona, Spain
[4] Az Osp Univ S Giovanni Battista Molinette, Turin, Italy
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
引用
收藏
页码:A104 / A104
页数:1
相关论文
共 50 条
  • [41] Generation of iPSC-based cardiomyocytes for investigating mechanisms of dilated cardiomyopathy
    Streckfuss-Boemeke, K.
    Tiburcy, M.
    Fomin, A.
    Fischer, C.
    Perrot, A.
    Oezcelik, C.
    Sossalla, S.
    Linke, W. A.
    Zimmermann, W.
    Hasenfuss, G.
    Guan, K.
    ACTA PHYSIOLOGICA, 2015, 213 : 23 - 24
  • [42] Comparing ESC and iPSC-Based Models for Human Genetic Disorders
    Halevy, Tomer
    Urbach, Achia
    JOURNAL OF CLINICAL MEDICINE, 2014, 3 (04): : 1146 - 1162
  • [43] A novel iPSC-based model of ICF syndrome subtype 2 recapitulates the molecular phenotype of ZBTB24 deficiency
    Lullo, Vincenzo
    Cecere, Francesco
    Batti, Saveria
    Allegretti, Sara
    Morone, Barbara
    Fioriniello, Salvatore
    Pisapia, Laura
    Genesio, Rita
    Della Ragione, Floriana
    Giardino, Giuliana
    Pignata, Claudio
    Riccio, Andrea
    Matarazzo, Maria R.
    Strazzullo, Maria
    FRONTIERS IN IMMUNOLOGY, 2024, 15
  • [44] Coated platelets and severe haemophilia A bleeding phenotype: Is there a connection?
    Lastrapes, K. K.
    Mohammed, B. M.
    Mazepa, M. A.
    Martin, E. J.
    Barrett, J. C.
    Massey, G. V.
    Kuhn, J. G.
    Nolte, M. E.
    Hoffman, M.
    Monroe, D. M.
    Brophy, D. F.
    HAEMOPHILIA, 2016, 22 (01) : 148 - 151
  • [45] Intracellular calcium current disorder and disease phenotype in OBSCN mutant iPSC-based cardiomyocytes in arrhythmogenic right ventricular cardiomyopathy
    Chen, Peipei
    Xiao, Ying
    Wang, Yuanpin
    Zheng, Zhifa
    Chen, Lianfeng
    Yang, Xufei
    Li, Jingyi
    Wu, Wei
    Zhang, Shuyang
    THERANOSTICS, 2020, 10 (24): : 11215 - 11229
  • [46] iPSC-Based Modeling of SCA12 for Targeted Therapeutic Screening
    Roy, R.
    Reddy, B.
    Gerutshang, A.
    Banerjee, R.
    Chowdhury, S.
    Kumar, H.
    Chattarji, S.
    MOVEMENT DISORDERS, 2024, 39 : S594 - S594
  • [47] Human iPSC-based Cardiac Microphysiological System For Drug Screening Applications
    Anurag Mathur
    Peter Loskill
    Kaifeng Shao
    Nathaniel Huebsch
    SoonGweon Hong
    Sivan G. Marcus
    Natalie Marks
    Mohammad Mandegar
    Bruce R. Conklin
    Luke P. Lee
    Kevin E. Healy
    Scientific Reports, 5
  • [48] iPSC-based disease modeling and drug discovery in cardinal neurodegenerative disorders
    Okano, Hideyuki
    Morimoto, Satoru
    CELL STEM CELL, 2022, 29 (02) : 189 - 208
  • [49] Omics analytical data sets for quality control of iPSC-based manufacturing
    Kim, Jung-Hyun
    Gil, Da Yeon
    TISSUE ENGINEERING PART A, 2022, 28 : 343 - 343
  • [50] Developing an iPSC-Based Therapeutic Approach to Reverse MPS IIIA Neurodegeneration
    Mandolfo, Oriana
    Bigger, Brian
    MOLECULAR THERAPY, 2022, 30 (04) : 345 - 345