Pre-clinical toxicology of AAV2/5-OPTIRPE65, an optimised RPE65 gene therapy vector

被引：0
|
作者：
Georgiadis, A. [1 ,3 ]
Duran, Y. [1 ]
Ribeiro, J. [1 ]
Abelleira, L. [1 ]
Naylor, S. [3 ]
Smith, A. J. [1 ,3 ]
Bainbridge, J. W. B. [1 ,2 ,3 ]
Ali, R. R. [1 ,2 ,3 ]
机构：
[1] UCL Inst Ophthalmol, London, England
[2] Moorfields Eye Hosp, NIHR Biomed Res Ctr, London, England
[3] MeiraGTx Ltd, London, England
来源：
HUMAN GENE THERAPY | 2017年 / 28卷 / 12期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P220
引用
收藏
页码：A77 / A77
页数：1
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