In Vivo Model to Evaluate Loss of Liver-Derived Factor IX Expression Caused by AAV Capsid-Specific CD8+T Cells

被引:0
|
作者
Markusic, David M. [1 ]
Martino, Ashley T. [2 ]
Mingozzi, Federico [3 ]
High, Katherine A.
Herzog, Roland W. [1 ]
机构
[1] Univ Florida, Gainesville, FL USA
[2] St Johns Univ, Dept Pharmaceut Sci, Queens, NY USA
[3] Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA
关键词
D O I
10.1182/blood.V120.21.2046.2046
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
2046
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页数:2
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