Second Generation Gene Therapy Vector for Classical Late Infantile Neuronal Ceroid Lipofuscinosis

被引：0

作者：

Cabrera-Salazar, Mario A. ^{[1
]}

Hodges, Bradley L. ^{[1
]}

Yew, Nelson S. ^{[1
]}

Bu, Jie ^{[1
]}

Fidler, Jonathan A. ^{[1
]}

Roskelley, Eric M. ^{[1
]}

Scheule, Ronald K. ^{[1
]}

Sleat, David E. ^{[2
]}

Lobel, Peter ^{[2
]}

Cheng, Seng H. ^{[1
]}

Passini, Marco A. ^{[1
]}

机构：

[1] Genzyme Corp, Appl Discovery Res & Neurosci, Framingham, MA 01701 USA

[2] Robert Wood Johnson Med Sch, Piscataway, NJ USA

来源：

MOLECULAR THERAPY | 2006年 / 13卷

关键词：

D O I：

10.1016/j.ymthe.2006.08.982

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

893

引用

页码：S344 / S344

页数：1

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