CRISPR/Cas9-Mediated Gene Knockout to Address Primary Hyperoxaluria

被引:0
|
作者
Huebner, Anette [1 ]
Wood, Kyle [2 ]
Dymek, Zachary [1 ]
Odate, Shobu [1 ]
Shaw, Cindy [1 ]
Krumm, Elizabeth [1 ]
Dowell, Alexander [2 ]
Doshi, Vinita [1 ]
Nolasco, Jonathan [1 ]
Wood, Kristy [1 ]
Strapps, Walter [1 ]
Finn, Jonathan D. [1 ]
Holmes, Ross [2 ]
Knight, John [2 ]
Burns, Sean [1 ]
机构
[1] Intellia Therapeut, Cambridge, MA USA
[2] Univ Alabama Birmingham, Birmingham, AL USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
1000
引用
收藏
页码:464 / 465
页数:2
相关论文
共 50 条
  • [21] Differences between immunodeficient mice generated by classical gene targeting and CRISPR/Cas9-mediated gene knockout
    Jae Hoon Lee
    Jong-Hyung Park
    Tae-Wook Nam
    Sun-Min Seo
    Jun-Young Kim
    Han-Kyul Lee
    Jong Hyun Han
    Song Yi Park
    Yang-Kyu Choi
    Han-Woong Lee
    [J]. Transgenic Research, 2018, 27 : 241 - 251
  • [22] CRISPR/Cas9-Mediated Gene Correction to Understand ALS
    Yun, Yeomin
    Ha, Yoon
    [J]. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2020, 21 (11)
  • [23] Pipeline for the generation of gene knockout mice using dual sgRNA CRISPR/Cas9-mediated gene editing
    Ghassemi, Bita
    Shamsara, Mehdi
    Soleimani, Masoud
    Kiani, Jafar
    Rassoulzadegan, Minoo
    [J]. ANALYTICAL BIOCHEMISTRY, 2019, 568 : 31 - 40
  • [24] Differences between immunodeficient mice generated by classical gene targeting and CRISPR/Cas9-mediated gene knockout
    Lee, Jae Hoon
    Park, Jong-Hyung
    Nam, Tae-Wook
    Seo, Sun-Min
    Kim, Jun-Young
    Lee, Han-Kyul
    Han, Jong Hyun
    Park, Song Yi
    Choi, Yang-Kyu
    Lee, Han-Woong
    [J]. TRANSGENIC RESEARCH, 2018, 27 (03) : 241 - 251
  • [25] CRISPR/Cas9-mediated knockout of myostatin in Chinese indigenous Erhualian pigs
    Wang, Kankan
    Tang, Xiaochun
    Xie, Zicong
    Zou, Xiaodong
    Li, Mengjing
    Yuan, Hongming
    Guo, Nannan
    Ouyang, Hongsheng
    Jiao, Huping
    Pang, Daxin
    [J]. TRANSGENIC RESEARCH, 2017, 26 (06) : 799 - 805
  • [26] Therapeutic potential of CRISPR/Cas9 mediated in vivo gene editing for primary hyperoxaluria
    Zabaleta, N.
    Barberia, M.
    Zapata-Linares, N.
    Rodriguez, S.
    Olaguee, C.
    Vales, A.
    Abizanda, G.
    Iglesias, E.
    Salido, E.
    Prosper, F.
    Gonzalez-Aseguinolaza, G.
    Rodriguez-Madoz, J. R.
    [J]. HUMAN GENE THERAPY, 2016, 27 (11) : A139 - A140
  • [27] The role of CRISPR/Cas9-mediated Drp1 knockout in ferroptosis
    Tang, S.
    Fuss, A.
    Zika, S.
    Culmsee, C.
    [J]. NAUNYN-SCHMIEDEBERGS ARCHIVES OF PHARMACOLOGY, 2022, 395 (SUPPL 1) : S57 - S57
  • [28] CRISPR/Cas9-mediated knockout of myostatin in Chinese indigenous Erhualian pigs
    Kankan Wang
    Xiaochun Tang
    Zicong Xie
    Xiaodong Zou
    Mengjing Li
    Hongming Yuan
    Nannan Guo
    Hongsheng Ouyang
    Huping Jiao
    Daxin Pang
    [J]. Transgenic Research, 2017, 26 : 799 - 805
  • [29] CRISPR/Cas9-mediated knockout strategies for enhancing immunotherapy in breast cancer
    Xu, Chenchen
    [J]. NAUNYN-SCHMIEDEBERGS ARCHIVES OF PHARMACOLOGY, 2024,
  • [30] CRISPR/Cas9-Mediated α-ENaC Knockout in a Murine Pancreatic β-Cell Line
    Zhang, Xue
    Zhao, Lihua
    Jin, Runbing
    Li, Min
    Li, Mei-Shuang
    Li, Rongfeng
    Liang, Xiubin
    [J]. FRONTIERS IN GENETICS, 2021, 12