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- [21] Relationship between Endogenous, Transgene FVIII Expression and Bleeding Events Following Valoctocogene Roxaparvovec Gene Transfer for Severe Hemophilia A: A Post-Hoc Analysis of the GENEr8-1 Phase 3 TrialBLOOD, 2021, 138Pipe, Steven W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAOzelo, Margareth C.论文数: 0 引用数: 0 h-index: 0机构: Univ Estadual Campinas, Sch Med Sci, Dept Internal Med, Hemocentro UNICAMP, Campinas, Brazil Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAKenet, Gili论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Natl Hemophilia Ctr, Sheba Med Ctr, Tel Aviv, Israel Tel Aviv Univ, Amalia Biron Res Inst Thrombosis & Haemostasis, Sheba Med Ctr, Tel Aviv, Israel Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAReding, Mark T.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Med Ctr, Ctr Bleeding & Clotting Disorders, Minneapolis, MN USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAMason, Jane论文数: 0 引用数: 0 h-index: 0机构: Univ Queensland, Brisbane, Qld, Australia Royal Brisbane & Womens Hosp, Queensland Haemophilia Ctr, Canc Care Serv, Brisbane, Qld, Australia Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USALeavitt, Andrew D.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Fransico, San Francisco, CA USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAMadan, Bella论文数: 0 引用数: 0 h-index: 0机构: Guys & St Thomas NHS Fdn Trust, London, England Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USALaffan, Michael论文数: 0 引用数: 0 h-index: 0机构: Imperial Coll London, Dept Med, Ctr Haematol, London, England Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAQuon, Doris V.论文数: 0 引用数: 0 h-index: 0机构: Orthopaed Hemophilia Treatment Ctr, Los Angeles, CA USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USADrygalski, Annettevon论文数: 0 引用数: 0 h-index: 0机构: Scripps Res Inst, Dept Mol Med, La Jolla, CA USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAChou, Sheng-Chieh论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ Hosp, Div Hematol, Dept Internal Med, Taipei, Taiwan Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAShapiro, Susan论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, Radcliffe Dept Med, Oxford, England Oxford Univ Hosp Natl Hlth Serv Fdn Trust, Oxford, England Natl Inst Hlth Res, Oxford Biomed Res Ctr, Oxford, England Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USADunn, Amy L.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Hemophilia Treatment Ctr, Columbus, OH USA Ohio State Univ, Coll Med, Columbus, OH USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAWang, Michael论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado, Hemophilia & Thrombosis Ctr, Anschutz Med Campus, Aurora, CO USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAKey, Nigel S.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, UNC Blood Res Ctr, Chapel Hill, NC USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAKaczmarek, Radoslaw论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ, Sch Med, IUPUI Wells Ctr Pediat Res, Dept Pediat, Indianapolis, IN USA Hirszfeld Inst Immunol & Expt Therapy, Lab Glycobiol, Wroclaw, Poland Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USASymington, Emily论文数: 0 引用数: 0 h-index: 0机构: Cambridge Univ Hosp NHS Fdn Trust, Cambridge, England Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USALawal, Adebayo论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceutical Inc, Novato, CA USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAMahajan, Reena论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceutical Inc, Novato, CA USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAChavele, Konstantia-Maria论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceutical Inc, Novato, CA USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAReddy, Divya B.论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceutical Inc, Novato, CA USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAYu, Hua论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceutical Inc, Novato, CA USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAWong, Wing Yen论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceutical Inc, Novato, CA USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USARobinson, Tara M.论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceutical Inc, Novato, CA USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USAKim, Benjamin论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceutical Inc, Novato, CA USA Univ Michigan, Dept Pediat & Pathol, Ann Arbor, MI USA
- [22] Real-time quantitative RT-PCR analysis of human T-cell lymphotropic virus type-1 (HTLV-I) tax mRNA: Correlation with HTLV-I proviral DNA load, Tax protein expression, Tax specific CD8+T-cell frequency and disease severity in patients with HTLV-I-associated myelopathy/tropical spastic paraparesis (HAM/TSP)AIDS RESEARCH AND HUMAN RETROVIRUSES, 2001, 17 : S25 - S25Yamano, Y论文数: 0 引用数: 0 h-index: 0机构: NINDS, Viral Immunol Sect, Neuroimmunol Branch, NIH, Bethesda, MD USANagai, M论文数: 0 引用数: 0 h-index: 0机构: NINDS, Viral Immunol Sect, Neuroimmunol Branch, NIH, Bethesda, MD USABrennan, MG论文数: 0 引用数: 0 h-index: 0机构: NINDS, Viral Immunol Sect, Neuroimmunol Branch, NIH, Bethesda, MD USAMora, CA论文数: 0 引用数: 0 h-index: 0机构: NINDS, Viral Immunol Sect, Neuroimmunol Branch, NIH, Bethesda, MD USASoldan, SS论文数: 0 引用数: 0 h-index: 0机构: NINDS, Viral Immunol Sect, Neuroimmunol Branch, NIH, Bethesda, MD USATomaru, U论文数: 0 引用数: 0 h-index: 0机构: NINDS, Viral Immunol Sect, Neuroimmunol Branch, NIH, Bethesda, MD USAOsame, M论文数: 0 引用数: 0 h-index: 0机构: NINDS, Viral Immunol Sect, Neuroimmunol Branch, NIH, Bethesda, MD USAJacobson, S论文数: 0 引用数: 0 h-index: 0机构: NINDS, Viral Immunol Sect, Neuroimmunol Branch, NIH, Bethesda, MD USA