共 50 条
- [21] Wild-type transthyretin cardiac amyloidosis: When is a rare disease no longer a rare disease? Journal of Nuclear Cardiology, 2021, 28 : 2857 - 2859
- [23] Drug reduces excess iron in ultra-rare neurodegenerative disease Nature Reviews Neurology, 2019, 15 : 492 - 493
- [28] Why we should care about ultra-rare disease EUROPEAN RESPIRATORY REVIEW, 2016, 25 (140): : 101 - 103