Multi-Institutional Assessments of Transplantation for Metabolic Disorders

被引:5
|
作者
Orchard, Paul [1 ]
Boelens, Jaap Jan [2 ]
Raymond, Gerald [3 ]
机构
[1] Univ Minnesota, Dept Pediat, Div Pediat Blood & Marrow Transplantat, Minneapolis, MN 55455 USA
[2] Univ Med Ctr Utrecht, Wilhelmina Childrens Hosp, Dept Pediat, Stem Cell Transplantat Unit, Utrecht, Netherlands
[3] Johns Hopkins Sch Med, Kennedy Krieger Inst, Dept Neurol, Baltimore, MD USA
关键词
X-LINKED ADRENOLEUKODYSTROPHY; HEMATOPOIETIC-CELL TRANSPLANTATION; CORD BLOOD TRANSPLANTATION; ENZYME REPLACEMENT THERAPY; STEM-CELL; PEDIATRIC-PATIENTS; ABNORMALITY; OUTCOMES; STORAGE; MANIFESTATIONS;
D O I
10.1016/j.bbmt.2012.10.026
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
[No abstract available]
引用
收藏
页码:S58 / S63
页数:6
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